Sickle cell-beta zero-thalassemia

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ORPHA:695140D57.2
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8Treatment centers1Financial resources

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Sickle cell-beta zero-thalassemia.

View clinical trials →

No actively recruiting trials found for Sickle cell-beta zero-thalassemia at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Sickle cell-beta zero-thalassemia community →

No specialists are currently listed for Sickle cell-beta zero-thalassemia.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

1 resources

CASGEVY

Vertex Pharmaceuticals / CRISPR Therapeutics

Sickle Cell Disease, Beta Thalassemia

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Patient Assistance
Patient Assistance
Accepting applications

Travel Grants

No travel grants are currently matched to Sickle cell-beta zero-thalassemia.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Sickle cell-beta zero-thalassemia

No recent news articles for Sickle cell-beta zero-thalassemia.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Sickle cell-beta zero-thalassemia

What treatment and support options exist for Sickle cell-beta zero-thalassemia?

1 patient support program are currently tracked on UniteRare for Sickle cell-beta zero-thalassemia. See the treatments and support programs sections for copay assistance, eligibility, and contact details.