Sex chromosome difference of sex development

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ORPHA:325546
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3Active trials2Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Sex chromosome difference of sex development (DSD) is a group of conditions where a person's sex chromosomes (the X and Y chromosomes) do not follow the typical XX (female) or XY (male) pattern, leading to differences in how the body develops sexually. Common examples include Turner syndrome (where a girl has only one X chromosome, written as 45,X), Klinefelter syndrome (where a boy has an extra X chromosome, written as 47,XXY), and mixed gonadal dysgenesis (where some cells have one chromosome pattern and others have a different one, such as 45,X/46,XY). These conditions can affect how the reproductive organs, hormones, and secondary sex characteristics (like breast development or facial hair) develop. Some people are diagnosed at birth because of differences in the appearance of the genitals, while others may not be diagnosed until puberty when expected changes do not occur, or even in adulthood when they have difficulty having children. Symptoms vary widely depending on the specific chromosome pattern and can include ambiguous genitalia, delayed or absent puberty, short stature, infertility, and differences in learning or behavior. Treatment is individualized and may include hormone replacement therapy, surgical options, fertility support, and psychological counseling. A team of specialists typically works together to provide comprehensive care tailored to each person's needs and preferences.

Also known as:

Key symptoms:

Ambiguous or atypical genitalia at birthDelayed puberty or absent pubertyShort stature or unusually tall statureInfertility or difficulty having childrenUndescended testiclesSmall testes or ovarian differencesBreast development in males (gynecomastia)Absent or irregular menstrual periodsDifferences in body proportionsLearning difficulties or attention problemsLow energy or fatigue related to hormone levelsBone density problems (osteoporosis)Heart or kidney differences (especially in Turner syndrome)Mood changes or anxiety

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

FDA & Trial Timeline

3 events
Apr 2025Long-term Systematic Follow-up of Patients With Klinefelter Syndrome Followed at the Department of Growth and Reproduction, Rigshospitalet

Rigshospitalet, Denmark

TrialENROLLING BY INVITATION
Aug 2024Klinefelter Syndrome and Testosterone Treatment in Puberty

Lise Aksglæde — PHASE4

TrialRECRUITING
Nov 2022Interrogating Fatty Acid Metabolism Impairment and Clinical Correlates in Males with Klinefelter Syndrome

University of Colorado, Denver — PHASE4

TrialACTIVE NOT RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Sex chromosome difference of sex development.

3 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

3 recruitingView all trials with filters →
Phase 42 trials
Klinefelter Syndrome and Testosterone Treatment in Puberty
Phase 4
Actively Recruiting
PI: Lise Aksglaede, MD (Copenhagen University Hospital, Rigshospitalet, Co) · Sites: Copenhagen · Age: 1014 yrs
Interrogating Fatty Acid Metabolism Impairment and Clinical Correlates in Males with Klinefelter Syndrome
Phase 4
Active
PI: Shanlee M Davis, MD, PhD (University of Colorado, Denver) · Sites: Aurora, Colorado · Age: 1540 yrs
Other1 trial
Long-term Systematic Follow-up of Patients With Klinefelter Syndrome Followed at the Department of Growth and Reproduction, Rigshospitalet
Enrolling by Invitation
· Sites: Copenhagen

Specialists

2 foundView all specialists →
NM
Nelly Mauras, MD
JACKSONVILLE, FL
Specialist
PI on 6 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Sex chromosome difference of sex development.

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Caregiver Resources

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Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is my (or my child's) exact chromosome pattern, and what does it mean for health and development?,Will hormone therapy be needed, and when should it start?,Is there any increased risk of tumors in the gonads, and how will this be monitored?,What are the options for fertility in the future?,Are there any heart, kidney, or bone health concerns that need regular screening?,Should we see a psychologist or counselor who specializes in differences of sex development?,Are there any decisions about surgery that need to be made now, or can they wait until the patient can participate in the decision?

Common questions about Sex chromosome difference of sex development

What is Sex chromosome difference of sex development?

Sex chromosome difference of sex development (DSD) is a group of conditions where a person's sex chromosomes (the X and Y chromosomes) do not follow the typical XX (female) or XY (male) pattern, leading to differences in how the body develops sexually. Common examples include Turner syndrome (where a girl has only one X chromosome, written as 45,X), Klinefelter syndrome (where a boy has an extra X chromosome, written as 47,XXY), and mixed gonadal dysgenesis (where some cells have one chromosome pattern and others have a different one, such as 45,X/46,XY). These conditions can affect how the re

How is Sex chromosome difference of sex development inherited?

Sex chromosome difference of sex development follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Sex chromosome difference of sex development?

Yes — 3 recruiting clinical trials are currently listed for Sex chromosome difference of sex development on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Sex chromosome difference of sex development?

2 specialists and care centers treating Sex chromosome difference of sex development are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.