Rh deficiency syndrome

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ORPHA:71275OMIM:617970D58.8
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1Specialists8Treatment centers

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Overview

Rh deficiency syndrome is a rare blood disorder where a person's red blood cells are missing or have very low levels of Rh proteins on their surface. These proteins are normally found on almost everyone's red blood cells and play an important role in keeping the cells healthy and properly shaped. When these proteins are absent or severely reduced, red blood cells become fragile and break down too easily — a process called hemolytic anemia. This means the body does not have enough healthy red blood cells to carry oxygen efficiently. People with Rh deficiency syndrome often have red blood cells that look abnormal under a microscope, appearing spiky or misshapen (called stomatocytes or spherocytes). The condition is sometimes called Rhnull disease when all Rh proteins are completely absent, or Rhmod disease when they are greatly reduced. Rhnull blood is sometimes called 'golden blood' because it is extremely rare and can be donated to almost anyone with Rh-related blood types. Symptoms can range from mild to moderate and include ongoing fatigue, pale skin, and yellowing of the skin or eyes (jaundice) due to red blood cell breakdown. Some people also develop an enlarged spleen. Treatment focuses on managing anemia, and in more severe cases, regular blood transfusions may be needed. Finding compatible blood for transfusions can be very challenging because Rhnull blood is so rare.

Also known as:

Key symptoms:

Ongoing tiredness and low energy (anemia)Pale or yellowish skinYellowing of the whites of the eyes (jaundice)Enlarged spleen (splenomegaly)Abnormally shaped red blood cells seen on blood testsShortness of breath, especially during activityRapid or irregular heartbeatDark-colored urine from red blood cell breakdownOccasional episodes of more severe anemiaGallstones at a younger age than usual (from chronic red blood cell breakdown)

Clinical phenotype terms (20)— hover any for plain English
Increased red cell osmotic fragilityHP:0005502Reduced haptoglobin levelHP:0020181Positive direct antiglobulin testHP:0032366SpherocytosisHP:0004444StomatocytosisHP:0004446HypochromiaHP:0032231AnisocytosisHP:0011273Macrocytic anemiaHP:0001972
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Rh deficiency syndrome.

View clinical trials →

No actively recruiting trials found for Rh deficiency syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Rh deficiency syndrome community →

Specialists

1 foundView all specialists →
LM
Lisa Dulli, PhD, MHS
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rh deficiency syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Rh deficiency syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

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Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How severe is my anemia, and do I need treatment right now or just monitoring?,Should I bank my own blood in case I ever need a transfusion, and how do I arrange that?,What should I do in a medical emergency if I need blood and compatible blood is not available?,Are my family members at risk, and should they be tested?,Are there any clinical trials or research studies I could join?,Should I take folic acid supplements, and are there other vitamins or lifestyle changes that could help?,Which hospitals or blood banks near me are best equipped to handle my rare blood type?

Common questions about Rh deficiency syndrome

What is Rh deficiency syndrome?

Rh deficiency syndrome is a rare blood disorder where a person's red blood cells are missing or have very low levels of Rh proteins on their surface. These proteins are normally found on almost everyone's red blood cells and play an important role in keeping the cells healthy and properly shaped. When these proteins are absent or severely reduced, red blood cells become fragile and break down too easily — a process called hemolytic anemia. This means the body does not have enough healthy red blood cells to carry oxygen efficiently. People with Rh deficiency syndrome often have red blood cells

How is Rh deficiency syndrome inherited?

Rh deficiency syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Which specialists treat Rh deficiency syndrome?

1 specialists and care centers treating Rh deficiency syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.