Renal dysplasia-megalocystis-sirenomelia syndrome

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:1850
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Renal dysplasia-megalocystis-sirenomelia syndrome is an extremely rare and severe birth defect condition that combines several major abnormalities present at birth. The name describes its three main features: renal dysplasia (where the kidneys do not develop properly), megalocystis (an abnormally enlarged bladder), and sirenomelia (a condition sometimes called 'mermaid syndrome' where the legs are fused together to varying degrees). Sirenomelia occurs when the lower body does not form correctly during early pregnancy, and it often comes along with serious problems in the kidneys, urinary tract, lower spine, and other organs. Babies born with this syndrome typically have life-threatening complications because the kidneys and urinary system are severely affected. The fused or malformed lower limbs also indicate major disruptions in how blood vessels and tissues developed in the lower half of the body. Other abnormalities may include problems with the genitals, anus, and lower intestine. Unfortunately, this condition is almost always fatal before or shortly after birth. There is no cure or effective treatment. Medical care focuses on supportive measures and compassionate care. Prenatal ultrasound can often detect the major features of this syndrome during pregnancy, which allows families to receive counseling and prepare. Because of the extreme severity and the involvement of multiple organ systems, long-term survival has not been reported in most cases.

Also known as:

Key symptoms:

Fused legs (mermaid-like lower limbs)Abnormally large bladderKidneys that did not develop properly or are absentAbsent or malformed anusAbsent or malformed genitalsSevere lack of amniotic fluid during pregnancy (oligohydramnios)Underdeveloped lungsAbnormal lower spine or absent sacrumSingle umbilical artery instead of twoAbsent or malformed lower intestineFlattened facial features due to low amniotic fluid (Potter sequence)

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Renal dysplasia-megalocystis-sirenomelia syndrome.

View clinical trials →

No actively recruiting trials found for Renal dysplasia-megalocystis-sirenomelia syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Renal dysplasia-megalocystis-sirenomelia syndrome community →

No specialists are currently listed for Renal dysplasia-megalocystis-sirenomelia syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Renal dysplasia-megalocystis-sirenomelia syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Renal dysplasia-megalocystis-sirenomelia syndromeForum →

No community posts yet. Be the first to share your experience with Renal dysplasia-megalocystis-sirenomelia syndrome.

Start the conversation →

Latest news about Renal dysplasia-megalocystis-sirenomelia syndrome

No recent news articles for Renal dysplasia-megalocystis-sirenomelia syndrome.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How certain is this diagnosis based on the ultrasound findings?,Would additional imaging like fetal MRI provide more information?,What are the options for the remainder of this pregnancy?,Is there any chance this could happen again in a future pregnancy?,Should we have genetic testing done, and what would it tell us?,What palliative care and comfort measures will be available for our baby?,Can you connect us with grief counseling or support groups for families in similar situations?

Common questions about Renal dysplasia-megalocystis-sirenomelia syndrome

What is Renal dysplasia-megalocystis-sirenomelia syndrome?

Renal dysplasia-megalocystis-sirenomelia syndrome is an extremely rare and severe birth defect condition that combines several major abnormalities present at birth. The name describes its three main features: renal dysplasia (where the kidneys do not develop properly), megalocystis (an abnormally enlarged bladder), and sirenomelia (a condition sometimes called 'mermaid syndrome' where the legs are fused together to varying degrees). Sirenomelia occurs when the lower body does not form correctly during early pregnancy, and it often comes along with serious problems in the kidneys, urinary tract

How is Renal dysplasia-megalocystis-sirenomelia syndrome inherited?

Renal dysplasia-megalocystis-sirenomelia syndrome follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Renal dysplasia-megalocystis-sirenomelia syndrome typically begin?

Typical onset of Renal dysplasia-megalocystis-sirenomelia syndrome is neonatal. Age of onset can vary across affected individuals.