RELA fusion-positive ependymoma

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Overview

RELA fusion-positive ependymoma is a type of brain tumor that grows in and around the fluid-filled spaces of the brain, called the ventricles. It belongs to a group of tumors called ependymomas, which arise from special cells that line these spaces. The 'RELA fusion' part means that inside the tumor cells, two genes have accidentally joined together — one of them is called RELA — creating an abnormal signal that drives tumor growth. This specific type most often occurs in the part of the brain above the brainstem, called the supratentorial region. It is also sometimes called 'ST-RELA ependymoma' or 'supratentorial ependymoma, RELA fusion-positive.' This tumor can press on brain tissue and block the normal flow of cerebrospinal fluid, the liquid that cushions the brain. This pressure causes many of the symptoms people experience. Common symptoms include headaches, nausea, vomiting, seizures, weakness on one side of the body, and changes in vision or behavior. In young children, the head may grow larger than expected. Treatment usually involves surgery to remove as much of the tumor as possible, followed by radiation therapy. Chemotherapy may also be used, especially in very young children or when the tumor comes back. Unfortunately, this type of ependymoma tends to be more aggressive than some other ependymoma types, and it has a higher chance of returning after treatment. Researchers are actively studying new targeted therapies aimed at the specific gene fusion that drives this tumor.

Also known as:

Key symptoms:

Frequent or severe headachesNausea and vomiting, especially in the morningSeizuresWeakness or numbness on one side of the bodyVision problems or double visionBalance and coordination difficultiesChanges in personality or behaviorDifficulty speaking or understanding wordsUnusual tiredness or low energyAbnormally large head size in infants and young childrenIncreased pressure inside the skull causing irritability in young children

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

Orphanet ↗NORD ↗

FDA & Trial Timeline

1 event
Aug 2019

ROZLYTREK: FDA approved

ROZLYTREK is indicated for the treatment of adult and pediatric patients 12 years of age and older with solid tumors that have a neurotrophic tyrosine receptor kinase (NTRK) gene fusion without a known acquired resistance mutation, are metastatic or where surgical resection is likely to result in severe morbidity, and have either progressed following treatment or have no satisfactory alternative therapy

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

ROZLYTREK

entrectinib· Genentech, Inc.Orphan Drug
ROZLYTREK is indicated for the treatment of adult and pediatric patients 12 years of age and older with solid tumors that have a neurotrophic tyrosine receptor kinase (NTRK) gene fusion without a know

ROZLYTREK is indicated for the treatment of adult and pediatric patients 12 years of age and older with solid tumors that have a neurotrophic tyrosine receptor kinase (NTRK) gene fusion without a known acquired resistance mutation, are metastatic or where surgical resection is likely to result in severe morbidity, and have either progressed following treatment or have no satisfactory alternative therapy

No actively recruiting trials found for RELA fusion-positive ependymoma at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the RELA fusion-positive ependymoma community →

Specialists

7 foundView all specialists →
HT
Hideo Takeshima
Specialist
1 RELA fusion-positive ependymoma publication
TF
Tsuyoshi Fukushima
Specialist
1 RELA fusion-positive ependymoma publication
FM
Fumitaka Matsumoto
Specialist
1 RELA fusion-positive ependymoma publication
MN
Mayumi Akaki Nagayasu
Specialist
1 RELA fusion-positive ependymoma publication
HK
Hiroaki Kataoka
Specialist
1 RELA fusion-positive ependymoma publication
YS
Yuichiro Sato
LA JOLLA, CA
Specialist
1 RELA fusion-positive ependymoma publication
GM
Giles W. Robinson, MD
MEMPHIS, TN
Specialist
PI on 4 active trials1 RELA fusion-positive ependymoma publication

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

1 resources

RETEVMO

Loxo Oncology Inc., a wholly owned subsidiary of Eli Lilly and Company

RETEVMO Patient Support (Lilly Cares)

Patient Assistance
Manufacturer Program
Accepting applications

Travel Grants

No travel grants are currently matched to RELA fusion-positive ependymoma.

Search all travel grants →NORD Financial Assistance ↗

Community

Open RELA fusion-positive ependymomaForum →

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Latest news about RELA fusion-positive ependymoma

No recent news articles for RELA fusion-positive ependymoma.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Was the RELA gene fusion confirmed by molecular testing, and what does this mean for my child's treatment plan?,How much of the tumor was removed during surgery, and does any tumor remain?,What type of radiation therapy is recommended, and what are the risks for my child's age and brain development?,Are there any clinical trials testing targeted therapies for RELA fusion-positive ependymoma that my child might qualify for?,How often will follow-up MRI scans be needed, and what are the warning signs of recurrence I should watch for at home?,What long-term side effects should we expect from treatment, and what specialists should we see to monitor for them?,What support services — such as neuropsychology testing, school support, or counseling — are available for our family?

Common questions about RELA fusion-positive ependymoma

What is RELA fusion-positive ependymoma?

RELA fusion-positive ependymoma is a type of brain tumor that grows in and around the fluid-filled spaces of the brain, called the ventricles. It belongs to a group of tumors called ependymomas, which arise from special cells that line these spaces. The 'RELA fusion' part means that inside the tumor cells, two genes have accidentally joined together — one of them is called RELA — creating an abnormal signal that drives tumor growth. This specific type most often occurs in the part of the brain above the brainstem, called the supratentorial region. It is also sometimes called 'ST-RELA ependymom

How is RELA fusion-positive ependymoma inherited?

RELA fusion-positive ependymoma follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does RELA fusion-positive ependymoma typically begin?

Typical onset of RELA fusion-positive ependymoma is childhood. Age of onset can vary across affected individuals.

Which specialists treat RELA fusion-positive ependymoma?

7 specialists and care centers treating RELA fusion-positive ependymoma are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for RELA fusion-positive ependymoma?

1 patient support program are currently tracked on UniteRare for RELA fusion-positive ependymoma. See the treatments and support programs sections for copay assistance, eligibility, and contact details.