Rare tumor of gallbladder and extrahepatic biliary tract

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2Active trials1Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Rare tumors of the gallbladder and extrahepatic biliary tract are uncommon growths that develop in the gallbladder or the bile ducts outside the liver. The biliary tract is the system of tubes that carries bile from the liver and gallbladder to the small intestine, where it helps digest fats. These rare tumors include unusual types that do not fall into the more common categories of gallbladder cancer (adenocarcinoma) or typical cholangiocarcinoma. They may include neuroendocrine tumors, sarcomas, lymphomas, granular cell tumors, and other very uncommon tumor types arising in these locations. Symptoms often develop slowly and may not appear until the tumor has grown large enough to block bile flow. Common signs include yellowing of the skin and eyes (jaundice), pain in the upper right abdomen, unexplained weight loss, nausea, and changes in stool color. Because these tumors are so rare, they can be difficult to diagnose and may be discovered incidentally during surgery for gallstones or other conditions. Treatment depends on the specific tumor type, its size, location, and whether it has spread. Surgery to remove the tumor is the primary treatment when possible. Chemotherapy, radiation therapy, or targeted therapies may also be used depending on the tumor subtype. Because of their rarity, treatment plans are often individualized, and patients may benefit from care at specialized cancer centers with experience in biliary tract tumors.

Also known as:

Key symptoms:

Yellowing of the skin and eyes (jaundice)Pain in the upper right side of the abdomenUnexplained weight lossNausea and vomitingLoss of appetitePale or clay-colored stoolsDark urineItchy skinA lump or mass in the abdomenFeverBloating or feeling full quicklyFatigue and general weakness

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

2 events
Oct 2024EUS-Gallbladder vs CDS as First Line in MBDO- Palliative (CARPEGIEM Trial)

Hospital Universitari de Bellvitge — NA

TrialRECRUITING
Jan 2021Basket Study of Tucatinib and Trastuzumab in Solid Tumors With HER2 Alterations

Seagen, a wholly owned subsidiary of Pfizer — PHASE2

TrialACTIVE NOT RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Rare tumor of gallbladder and extrahepatic biliary tract.

2 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

2 recruitingView all trials with filters →
Phase 21 trial
Basket Study of Tucatinib and Trastuzumab in Solid Tumors With HER2 Alterations
Phase 2
Active
PI: Pfizer CT.gov Call Center (Pfizer) · Sites: Phoenix, Arizona; Tempe, Arizona +104 more · Age: 1899 yrs
N/A1 trial
EUS-Gallbladder vs CDS as First Line in MBDO- Palliative (CARPEGIEM Trial)
N/A
Actively Recruiting
PI: Joan B Gornals Soler (Study Principal Investigator) · Sites: L'Hospitalet de Llobregat, BARCELONA; Alicante, Valencia +8 more · Age: 18100 yrs

Specialists

1 foundView all specialists →
SP
Sandip P Patel
Birmingham, Alabama
Specialist

Rare Disease Specialist

PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

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Community

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific type of rare tumor do I have, and how does that affect my treatment options?,Has molecular or genetic testing been done on my tumor, and are there any targeted therapies that might work for me?,Is surgery an option for my tumor, and what would that involve?,Are there any clinical trials available for my specific tumor type?,What are the expected side effects of the recommended treatment?,Should I seek a second opinion at a specialized hepatobiliary cancer center?,What supportive care services are available to help me manage symptoms and quality of life?

Common questions about Rare tumor of gallbladder and extrahepatic biliary tract

What is Rare tumor of gallbladder and extrahepatic biliary tract?

Rare tumors of the gallbladder and extrahepatic biliary tract are uncommon growths that develop in the gallbladder or the bile ducts outside the liver. The biliary tract is the system of tubes that carries bile from the liver and gallbladder to the small intestine, where it helps digest fats. These rare tumors include unusual types that do not fall into the more common categories of gallbladder cancer (adenocarcinoma) or typical cholangiocarcinoma. They may include neuroendocrine tumors, sarcomas, lymphomas, granular cell tumors, and other very uncommon tumor types arising in these locations.

How is Rare tumor of gallbladder and extrahepatic biliary tract inherited?

Rare tumor of gallbladder and extrahepatic biliary tract follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Rare tumor of gallbladder and extrahepatic biliary tract typically begin?

Typical onset of Rare tumor of gallbladder and extrahepatic biliary tract is adult. Age of onset can vary across affected individuals.

Are there clinical trials for Rare tumor of gallbladder and extrahepatic biliary tract?

Yes — 2 recruiting clinical trials are currently listed for Rare tumor of gallbladder and extrahepatic biliary tract on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Rare tumor of gallbladder and extrahepatic biliary tract?

1 specialists and care centers treating Rare tumor of gallbladder and extrahepatic biliary tract are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.