Rare genetic venous malformation

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Overview

Rare genetic venous malformation is an uncommon condition where veins in the body develop abnormally due to changes (mutations) in specific genes. Venous malformations are a type of vascular anomaly, meaning they involve blood vessels that did not form correctly during development. These malformations are made up of abnormally widened and tangled veins that can appear as soft, bluish lumps under the skin or within deeper tissues and organs. They are typically present at birth, though they may not always be noticed right away and can grow slowly over time. The symptoms depend on where the malformation is located and how large it is. Common problems include pain, swelling, and a visible bluish discoloration of the skin. Some venous malformations can cause blood clots within the abnormal veins, leading to localized pain and hardness. In more severe cases, large or widespread malformations can affect the function of nearby muscles, joints, or organs. Some patients may experience bleeding or problems with blood clotting. Treatment is tailored to each patient and may include compression garments, pain management, sclerotherapy (injecting a substance to shrink the malformation), and sometimes surgery. Newer targeted therapies, such as drugs that block specific signaling pathways involved in abnormal vessel growth, are being studied and used in some cases. Because this is a genetic condition, genetic counseling is recommended for affected individuals and their families.

Key symptoms:

Soft bluish lumps or swelling under the skinPain in the affected area, especially with activitySwelling that may worsen when standing or with exertionBluish or purplish skin discolorationBlood clots forming within the malformation (causing hard, painful lumps)Stiffness or limited movement in nearby jointsMuscle weakness near the malformationBleeding from the malformationEnlargement of the affected area over timeFatigue or tirednessProblems with blood clotting (low-grade coagulopathy)Disfigurement or cosmetic concerns

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Rare genetic venous malformation.

View clinical trials →

No actively recruiting trials found for Rare genetic venous malformation at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Rare genetic venous malformation community →

No specialists are currently listed for Rare genetic venous malformation.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rare genetic venous malformation.

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Community

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Latest news about Rare genetic venous malformation

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What gene mutation is causing my (or my child's) venous malformation, and does it affect treatment options?,How often should we have imaging done to monitor the malformation?,Is sclerotherapy or surgery recommended in our case, and what are the risks?,Would a targeted therapy like sirolimus be appropriate, and what are the potential side effects?,Are there any activities or situations we should avoid to prevent complications?,Should other family members be tested for this genetic condition?,Are there any clinical trials we should consider?

Common questions about Rare genetic venous malformation

What is Rare genetic venous malformation?

Rare genetic venous malformation is an uncommon condition where veins in the body develop abnormally due to changes (mutations) in specific genes. Venous malformations are a type of vascular anomaly, meaning they involve blood vessels that did not form correctly during development. These malformations are made up of abnormally widened and tangled veins that can appear as soft, bluish lumps under the skin or within deeper tissues and organs. They are typically present at birth, though they may not always be noticed right away and can grow slowly over time. The symptoms depend on where the malf

At what age does Rare genetic venous malformation typically begin?

Typical onset of Rare genetic venous malformation is neonatal. Age of onset can vary across affected individuals.