Rare genetic movement disorder

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ORPHA:183521
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11Specialists8Treatment centers

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Overview

Orphanet entry 183521 refers to a rare genetic movement disorder, but this specific code does not correspond to a widely characterized or well-documented condition in the publicly available medical literature. Rare genetic movement disorders are a broad group of conditions that affect the brain's ability to control body movements. These disorders can cause symptoms such as involuntary movements (like tremors, jerks, or twisting), difficulty coordinating movements, stiffness, or problems with balance and walking. They are caused by changes (mutations) in genes that play important roles in how nerve cells communicate and control movement. Because this particular Orphanet code does not map to a condition with extensive published clinical data, specific details about its exact genetic cause, natural history, and treatment options are limited. Patients and families who have received a diagnosis linked to this code should work closely with a clinical geneticist and a movement disorder neurologist to get the most up-to-date and personalized information. Treatment for rare genetic movement disorders is often supportive and symptom-based, and may include medications to reduce abnormal movements, physical therapy, occupational therapy, and sometimes surgical options like deep brain stimulation depending on the specific condition.

Key symptoms:

Involuntary movements such as tremors or jerksDifficulty with coordination and balanceMuscle stiffness or rigidityTwisting or repetitive movements (dystonia)Difficulty walking or unsteady gaitSlow movementsSpeech difficultiesTrouble with fine motor tasks like writing or buttoning clothesFatigueDifficulty swallowing in some cases

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Rare genetic movement disorder.

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No actively recruiting trials found for Rare genetic movement disorder at this time.

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Specialists

11 foundView all specialists →
BR
Belen Ruiz-Antorán
Specialist
PI on 1 active trial
AM
Alan Percy, MD
BIRMINGHAM, AL
Specialist
PI on 4 active trials
PC
Pier Luigi Carriero
Specialist
PI on 1 active trial
LP
Luca Sangiorgi, MD, PhD
Bologna, Emilia-Romagna
Specialist

Rare Disease Specialist

PI on 2 active trials
MP
Marcelo Serra, PhD
Buenos Aires, Buenos Aires
Specialist

Rare Disease Specialist

PI on 1 active trial
AP
Anna Jansen, MD, PhD
Silver Spring, Maryland
Specialist

Rare Disease Specialist

PI on 2 active trials
MP
Maria Lourdes Posadas Martinez, PhD
Specialist
PI on 1 active trial
RP
Rosanna Cardani, PhD
San Donato Milanese, Milan
Specialist

Rare Disease Specialist

PI on 1 active trial
SM
Sanjeev Kothare, MD
NEW HYDE PARK, NY
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rare genetic movement disorder.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Rare genetic movement disorder

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific genetic test should we pursue to confirm the diagnosis?,Are there any medications that could help control the movement symptoms?,What therapies (physical, occupational, speech) would benefit my condition?,Is this condition expected to get worse over time, or could it remain stable?,Are there any clinical trials or research studies we could participate in?,Should other family members be tested for this genetic condition?,What emergency signs should we watch for, and when should we go to the hospital?

Common questions about Rare genetic movement disorder

What is Rare genetic movement disorder?

Orphanet entry 183521 refers to a rare genetic movement disorder, but this specific code does not correspond to a widely characterized or well-documented condition in the publicly available medical literature. Rare genetic movement disorders are a broad group of conditions that affect the brain's ability to control body movements. These disorders can cause symptoms such as involuntary movements (like tremors, jerks, or twisting), difficulty coordinating movements, stiffness, or problems with balance and walking. They are caused by changes (mutations) in genes that play important roles in how n

Which specialists treat Rare genetic movement disorder?

11 specialists and care centers treating Rare genetic movement disorder are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.