Rare genetic autonomic nervous system disorder

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:434786
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Rare genetic autonomic nervous system disorder (Orphanet code 434786) refers to a group of uncommon inherited conditions that affect the autonomic nervous system — the part of your nervous system that controls automatic body functions you don't consciously think about. These include heart rate, blood pressure, sweating, digestion, bladder function, and temperature regulation. Because the autonomic nervous system touches so many parts of the body, symptoms can be wide-ranging and affect multiple organ systems. People with these disorders may experience problems such as fainting or dizziness when standing up (due to drops in blood pressure), abnormal sweating (too much or too little), digestive difficulties like nausea or constipation, trouble controlling body temperature, and irregular heart rhythms. The severity can vary greatly from person to person, even within the same family. Treatment is generally focused on managing symptoms, as there is currently no cure for most genetic autonomic disorders. This may include medications to raise blood pressure, dietary changes such as increased salt and fluid intake, physical countermaneuvers, and careful monitoring by a team of specialists. Early diagnosis through genetic testing can help guide treatment and allow families to plan appropriately. Research into these conditions is ongoing, and new therapies are being explored.

Key symptoms:

Dizziness or fainting when standing upAbnormal blood pressure changesRapid or irregular heartbeatExcessive or absent sweatingDifficulty regulating body temperatureChronic constipation or digestive problemsNausea or vomitingBladder control problemsDry eyes or dry mouthBlurred visionFatigue and low energyExercise intoleranceNumbness or tingling in hands and feetDifficulty swallowing

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Rare genetic autonomic nervous system disorder.

View clinical trials →

No actively recruiting trials found for Rare genetic autonomic nervous system disorder at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Rare genetic autonomic nervous system disorder community →

No specialists are currently listed for Rare genetic autonomic nervous system disorder.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rare genetic autonomic nervous system disorder.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Rare genetic autonomic nervous system disorderForum →

No community posts yet. Be the first to share your experience with Rare genetic autonomic nervous system disorder.

Start the conversation →

Latest news about Rare genetic autonomic nervous system disorder

No recent news articles for Rare genetic autonomic nervous system disorder.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific type of genetic autonomic disorder do I or my child have, and which gene is affected?,What symptoms should I watch for that would require emergency care?,Are there medications that can help manage blood pressure drops or other symptoms?,Should other family members be tested for this condition?,Are there any clinical trials or new treatments being studied for this condition?,What lifestyle changes can help manage symptoms day to day?,How often should I have follow-up testing to monitor how the condition is progressing?

Common questions about Rare genetic autonomic nervous system disorder

What is Rare genetic autonomic nervous system disorder?

Rare genetic autonomic nervous system disorder (Orphanet code 434786) refers to a group of uncommon inherited conditions that affect the autonomic nervous system — the part of your nervous system that controls automatic body functions you don't consciously think about. These include heart rate, blood pressure, sweating, digestion, bladder function, and temperature regulation. Because the autonomic nervous system touches so many parts of the body, symptoms can be wide-ranging and affect multiple organ systems. People with these disorders may experience problems such as fainting or dizziness wh