Rare diabetes mellitus | UniteRare Disease Library

Overview

Orphanet ↗NORD ↗

FDA & Trial Timeline

5 events

Jan 2026Gamification Intervertion in Children With Type 1 Diabetes

KTO Karatay University — NA

TrialRECRUITING

Jan 2026Lifestyle Interventions to Prevent Diabetes in U.S. Home Visiting Programs

California Polytechnic State University-San Luis Obispo — NA

TrialRECRUITING

Nov 2025Understanding Beta Cell Disorders Through the Study of Rare Genotypes (ENDURE)

University of Exeter

TrialRECRUITING

Mar 2022Effects of Tirzepatide and Insulin Glargine on Glucolipid Metabolism and Brain Function in Patients With Type 2 Diabetes

Nanjing First Hospital, Nanjing Medical University — PHASE4

TrialRECRUITING

Sep 2020Rare and Atypical Diabetes Network

University of South Florida

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Rare diabetes mellitus.

3 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

3 recruitingView all trials with filters →

N/A1 trial

Lifestyle Interventions to Prevent Diabetes in U.S. Home Visiting Programs

N/A

Actively Recruiting

PI: Suzanne Phelan, PhD (California Polytechnic State University-San Luis O) · Sites: San Luis Obispo, California; Chicago, Illinois +1 more · Age: 18–99 yrs

Other2 trials

Rare and Atypical Diabetes Network

Actively Recruiting

PI: Jeffrey Krischer, PhD (University of South Florida) · Sites: Aurora, Colorado; Chicago, Illinois +11 more

Understanding Beta Cell Disorders Through the Study of Rare Genotypes (ENDURE)

Actively Recruiting

PI: Andrew Hattersley, FRS, FMed (University of Exeter) · Sites: Exeter, Devon · Age: 6–99 yrs

Specialists

8 foundView all specialists →

Laura M Koehly, Ph.D.

Specialist

CLN3 disease Familial hypocalciuric hypercalcemia Familial hypocalciuric hypercalcemia type 1+14 more

PI on 5 active trials

Active trials Directions Travel grants

Jeffrey Krischer, PhD

Specialist

Gangliosidosis GM2 gangliosidosis Sandhoff disease+2 more

PI on 3 active trials

Active trials Directions Travel grants

Timothy M Frayling (Prof), PhD

Specialist

Rare diabetes mellitus type 1 Rare diabetes mellitus type 2 Rare genetic diabetes mellitus+2 more

PI on 1 active trial

Active trials Directions Travel grants

Andrew Hattersley, FRS, FMed

Specialist

Rare genetic diabetes mellitus Rare genetic endocrine disease

PI on 1 active trial

Active trials Directions Travel grants

Daniele o Provenzano, md

Specialist

Rare bacterial infectious disease Rare diabetes mellitus type 2 Rare mycosis

PI on 1 active trial

Active trials Directions Travel grants

Suzanne Phelan, PhD

San Luis Obispo, California

Specialist

Rare Disease Specialist

Directions Travel grants

Jianhua Ma, Doctor

Nanjing, Jiangsu

Specialist

Rare Disease Specialist

Directions Travel grants

Gülfidan Başer

Ankara, Yenimahalle

Specialist

Rare Disease Specialist

Directions Travel grants

Treatment Centers

8 centers

⚗️ Trial Site

Northwestern University

📍 Chicago, Illinois

👤 Ann (Annie) W Silk

🏥 NORD

Stanford Medicine Rare Disease Center ↗

Stanford Medicine

📍 Stanford, CA

🏥 NORD

Mayo Clinic Center for Individualized Medicine ↗

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🔬 UDN

UCLA UDN Clinical Site ↗

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site ↗

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site ↗

Massachusetts General Hospital

📍 Boston, MA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program ↗

National Institutes of Health

📍 Bethesda, MD

🏥 NORD

Baylor College of Medicine Rare Disease Center ↗

Baylor College of Medicine

📍 Houston, TX

Travel Grants

No travel grants are currently matched to Rare diabetes mellitus.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Rare diabetes mellitus

Disease timeline:

New recruiting trial: Understanding Beta Cell Disorders Through the Study of Rare Genotypes (ENDURE)

A new clinical trial is recruiting patients for Rare diabetes mellitus

New recruiting trial: Rare and Atypical Diabetes Network

A new clinical trial is recruiting patients for Rare diabetes mellitus

New trial: Effects of Tirzepatide and Insulin Glargine on Glucolipid Metabolism and Brain Function in Patients

Phase PHASE4 trial recruiting. Tirzepatide

New trial: Gamification Intervertion in Children With Type 1 Diabetes

Phase NA trial recruiting. Gamification

New trial: Lifestyle Interventions to Prevent Diabetes in U.S. Home Visiting Programs

Phase NA trial recruiting. GDM Enhanced

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Rare diabetes mellitus

Are there clinical trials for Rare diabetes mellitus?

Yes — 3 recruiting clinical trials are currently listed for Rare diabetes mellitus on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Rare diabetes mellitus?

8 specialists and care centers treating Rare diabetes mellitus are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.