Pure or complex autosomal recessive spastic paraplegia

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Overview

Pure or complex autosomal recessive spastic paraplegia is a group of inherited neurological conditions that primarily affect the nerves controlling leg movement. The hallmark feature is progressive stiffness (spasticity) and weakness in the legs, which makes walking increasingly difficult over time. In 'pure' forms, the symptoms are mainly limited to the legs, with stiffness, weakness, and sometimes bladder problems. In 'complex' forms, additional neurological problems occur, such as intellectual disability, seizures, vision or hearing problems, nerve damage in the hands and feet, difficulty with balance, or thinning of certain brain structures. These conditions are caused by mutations in various genes that are important for the health and function of the long nerve fibers (axons) in the spinal cord. Because the inheritance is autosomal recessive, a child must inherit a faulty copy of the gene from both parents to develop the disease. Parents who each carry one faulty copy typically do not show symptoms themselves. There is currently no cure for autosomal recessive spastic paraplegia. Treatment focuses on managing symptoms and maintaining mobility for as long as possible. This includes physical therapy, medications to reduce muscle stiffness, assistive devices like braces or walkers, and sometimes surgery. Research is ongoing to better understand the many genetic causes and to develop targeted therapies.

Also known as:

Key symptoms:

Progressive leg stiffness (spasticity)Difficulty walkingLeg weaknessFrequent tripping or fallingBladder urgency or incontinenceNumbness or tingling in the feetBalance problemsIntellectual disability (in complex forms)Seizures (in complex forms)Vision problems (in complex forms)Hearing loss (in complex forms)Difficulty with fine hand movementsSpeech difficulties (in complex forms)Thinning of the corpus callosum on brain MRI (in complex forms)Muscle wasting in the legs

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Pure or complex autosomal recessive spastic paraplegia.

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No actively recruiting trials found for Pure or complex autosomal recessive spastic paraplegia at this time.

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No specialists are currently listed for Pure or complex autosomal recessive spastic paraplegia.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Pure or complex autosomal recessive spastic paraplegia.

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.What specific genetic subtype of spastic paraplegia does my family member have, and what does that mean for the expected course of the disease?,What therapies and medications are recommended to manage spasticity and maintain mobility?,Are there any clinical trials or research studies we should consider?,How often should we schedule follow-up visits with neurology and other specialists?,Should other family members be tested as carriers of this condition?,What assistive devices or home modifications would be helpful at this stage?,Are there any complications we should watch for that would need urgent medical attention?

Common questions about Pure or complex autosomal recessive spastic paraplegia

What is Pure or complex autosomal recessive spastic paraplegia?

Pure or complex autosomal recessive spastic paraplegia is a group of inherited neurological conditions that primarily affect the nerves controlling leg movement. The hallmark feature is progressive stiffness (spasticity) and weakness in the legs, which makes walking increasingly difficult over time. In 'pure' forms, the symptoms are mainly limited to the legs, with stiffness, weakness, and sometimes bladder problems. In 'complex' forms, additional neurological problems occur, such as intellectual disability, seizures, vision or hearing problems, nerve damage in the hands and feet, difficulty w

How is Pure or complex autosomal recessive spastic paraplegia inherited?

Pure or complex autosomal recessive spastic paraplegia follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.