Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:431353
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis (PVOD/PCH) is a rare and serious lung condition that affects the small blood vessels inside the lungs. In PVOD, the tiny veins that carry blood away from the lungs become blocked or scarred, making it very hard for blood to flow properly. In PCH, abnormal small blood vessels grow out of control inside the lung tissue. These two conditions are closely related and often overlap, which is why they are grouped together. Both lead to a dangerous rise in blood pressure inside the lungs, a condition called pulmonary arterial hypertension (PAH). As the disease progresses, the heart has to work much harder to pump blood through the lungs. Over time, this strains the right side of the heart and can lead to heart failure. People with PVOD/PCH often feel very short of breath, especially during activity, and may feel extremely tired even at rest. Other symptoms include a persistent cough, low oxygen levels in the blood, and fluid buildup in the body. Treatment is very challenging. Most standard pulmonary hypertension medications can actually make PVOD/PCH worse by causing dangerous fluid to build up in the lungs. The only known cure is a lung transplant. Some patients with a genetic form of the disease caused by changes in the EIF2AK4 gene may be identified earlier through genetic testing. Research into better treatments is ongoing, but this remains one of the most difficult forms of pulmonary hypertension to manage.

Key symptoms:

Shortness of breath, especially during physical activityExtreme tiredness and fatiguePersistent dry coughLow oxygen levels in the bloodBluish tint to the lips or fingertips (cyanosis)Swelling in the legs, ankles, or feetFainting or near-fainting spellsChest pain or pressureRapid or irregular heartbeatReduced ability to exercise or do daily activitiesFluid buildup in the lungs (pulmonary edema)Clubbing of the fingers (rounded, enlarged fingertips)

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis.

View clinical trials →

No actively recruiting trials found for Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis community →

No specialists are currently listed for Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosisForum →

No community posts yet. Be the first to share your experience with Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis.

Start the conversation →

Latest news about Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis

No recent news articles for Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Should I have genetic testing for the EIF2AK4 gene, and what would a positive result mean for me and my family?,Am I a candidate for lung transplantation, and when should I be referred to a transplant center?,Which pulmonary hypertension medications are safe for me, and which ones should I avoid?,How often should I have follow-up tests, and what signs of worsening should I watch for at home?,What oxygen therapy do I need, and how will this change as my disease progresses?,Are there any clinical trials I could join?,What support services — such as social work, pulmonary rehabilitation, or mental health support — are available to me?

Common questions about Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis

What is Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis?

Pulmonary veno-occlusive disease and/or pulmonary capillary haemangiomatosis (PVOD/PCH) is a rare and serious lung condition that affects the small blood vessels inside the lungs. In PVOD, the tiny veins that carry blood away from the lungs become blocked or scarred, making it very hard for blood to flow properly. In PCH, abnormal small blood vessels grow out of control inside the lung tissue. These two conditions are closely related and often overlap, which is why they are grouped together. Both lead to a dangerous rise in blood pressure inside the lungs, a condition called pulmonary arterial