Primary triglyceride deposit cardiomyovasculopathy

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2Specialists8Treatment centers

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Overview

Primary triglyceride deposit cardiomyovasculopathy, sometimes called TGCV or triglyceride deposit cardiomyovasculopathy, is a rare inherited disease where fat — specifically a type called triglycerides — builds up abnormally inside the heart muscle and blood vessel walls. This buildup happens because the body cannot properly break down triglycerides inside cells, leading to a harmful accumulation over time. The disease mainly affects the heart and blood vessels, causing the heart muscle to weaken and the arteries to become stiff and narrowed. People with this condition often develop a form of heart failure called dilated cardiomyopathy, where the heart becomes enlarged and pumps blood less effectively. They may also develop coronary artery disease at a younger age than expected, even without the usual risk factors like high cholesterol or smoking. Muscle weakness affecting the body's skeletal muscles can also occur in some people. Treatment today focuses on managing heart failure symptoms and protecting the heart, using standard heart medications. There is currently no approved cure or therapy that directly removes the triglyceride deposits. Research into targeted treatments is ongoing, and early diagnosis is important to slow the progression of heart damage.

Also known as:

Key symptoms:

Shortness of breath, especially during activityFatigue and low energySwelling in the legs, ankles, or feetIrregular or rapid heartbeat (palpitations)Chest pain or pressureEnlarged, weakened heart (dilated cardiomyopathy)Narrowing of the heart's arteries (coronary artery disease)Muscle weakness in the arms or legsReduced ability to exerciseDizziness or lightheadedness

Clinical phenotype terms (29)— hover any for plain English
Vacuolated lymphocytesHP:0001922Skeletal myopathyHP:0003756Increased muscle lipid contentHP:0009058Abnormal cardiomyocyte morphologyHP:0031331Abnormal calf musculature morphologyHP:0001430Abnormality of the shoulder girdle musculatureHP:0001435Coronary artery atherosclerosisHP:0001677Coronary artery stenosisHP:0005145Low-output congestive heart failureHP:0009805Precordial painHP:0032141
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Primary triglyceride deposit cardiomyovasculopathy.

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No actively recruiting trials found for Primary triglyceride deposit cardiomyovasculopathy at this time.

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Specialists

2 foundView all specialists →

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

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Community

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Caregiver Resources

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Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What stage is my heart disease at, and how quickly might it progress?,Should my family members be tested for the PNPLA2 gene change?,Which heart medications are best for my situation, and what side effects should I watch for?,Do I need a defibrillator or other device to protect my heart rhythm?,Are there any clinical trials or experimental treatments I should consider?,What physical activities are safe for me, and which should I avoid?,How often do I need heart imaging and follow-up appointments?

Common questions about Primary triglyceride deposit cardiomyovasculopathy

What is Primary triglyceride deposit cardiomyovasculopathy?

Primary triglyceride deposit cardiomyovasculopathy, sometimes called TGCV or triglyceride deposit cardiomyovasculopathy, is a rare inherited disease where fat — specifically a type called triglycerides — builds up abnormally inside the heart muscle and blood vessel walls. This buildup happens because the body cannot properly break down triglycerides inside cells, leading to a harmful accumulation over time. The disease mainly affects the heart and blood vessels, causing the heart muscle to weaken and the arteries to become stiff and narrowed. People with this condition often develop a form of

How is Primary triglyceride deposit cardiomyovasculopathy inherited?

Primary triglyceride deposit cardiomyovasculopathy follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Primary triglyceride deposit cardiomyovasculopathy typically begin?

Typical onset of Primary triglyceride deposit cardiomyovasculopathy is adult. Age of onset can vary across affected individuals.

Which specialists treat Primary triglyceride deposit cardiomyovasculopathy?

2 specialists and care centers treating Primary triglyceride deposit cardiomyovasculopathy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.