Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments

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Overview

Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments is an extremely rare condition in which the body gradually turns soft tissues — such as skin, muscles, tendons, ligaments, and the thin tissue covering muscles (fascia) — into bone. This abnormal bone formation process is called heterotopic ossification. The disease typically begins with skeletal abnormalities present from birth or early childhood, including malformed bones and restricted joint movement. Over time, sheets and plates of new bone form within soft tissues throughout the body, severely limiting movement and function. This condition is closely related to, and may overlap with, fibrodysplasia ossificans progressiva (FOP), but it is classified separately because of its distinct features involving primary bone dysplasia (abnormal development of the skeleton itself) alongside the progressive ossification of soft tissues. Patients may notice painful swelling or flare-ups in muscles or under the skin that eventually harden into bone. Trauma, surgery, or even minor injuries can trigger new episodes of bone formation. There is currently no cure for this condition. Treatment focuses on managing symptoms, preventing flare-ups, and maintaining quality of life. Avoiding unnecessary trauma, including intramuscular injections and invasive procedures, is critical. Research into medications that may slow or prevent abnormal bone formation is ongoing, but options remain very limited. Supportive care from a multidisciplinary team of specialists is essential for managing this progressive and disabling disease.

Also known as:

Key symptoms:

Abnormal bone development from birthProgressive hardening and bone formation in musclesBone forming in the skinStiffening and loss of movement in jointsPainful swelling or lumps in soft tissuesRestricted movement of the jaw making eating difficultDifficulty breathing due to chest wall stiffnessMalformed or shortened fingers and toesMalformed big toesCurved spine (scoliosis)Difficulty walking or inability to walkBone forming in tendons and ligamentsProgressive loss of independenceFlare-ups triggered by injury or trauma

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments.

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No actively recruiting trials found for Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments at this time.

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No specialists are currently listed for Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments.

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Community

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific genetic mutation is causing this condition in my case?,How can we best prevent flare-ups and new bone formation?,Are there any clinical trials or new treatments I should know about?,What should I do if I notice new swelling or a painful lump?,How should we monitor my breathing and lung function over time?,What types of physical activity are safe, and what should be avoided?,Are there any medications, injections, or procedures I should specifically avoid?

Common questions about Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments

What is Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments?

Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments is an extremely rare condition in which the body gradually turns soft tissues — such as skin, muscles, tendons, ligaments, and the thin tissue covering muscles (fascia) — into bone. This abnormal bone formation process is called heterotopic ossification. The disease typically begins with skeletal abnormalities present from birth or early childhood, including malformed bones and restricted joint movement. Over time, sheets and plates of new bone form within soft tissues throughout the bo

At what age does Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments typically begin?

Typical onset of Primary bone dysplasia with progressive ossification of skin, skeletal muscle, fascia, tendons and ligaments is childhood. Age of onset can vary across affected individuals.