Treatments for Pompe disease

FDA-approved drugs, patient assistance programs, and travel grants tracked on UniteRare for this condition.

Treatment data is extracted from FDA drug labels, DailyMed, and openFDA through automated and AI-assisted pipelines that read both structured records and unstructured label text.
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FDA-approved treatments (3)

Patient support programs (6)

Copay cards, manufacturer assistance, and foundation grants. Verification status shown on each card.

NORD Patient Assistance — Pompe disease

NORD Patient Assistance

Pompe disease

Verified 32d ago
Foundation Grant
foundation grant
Accepting applications
Apply

The Assistance Fund — Pompe disease

The Assistance Fund

Pompe disease

Verified 32d ago
Foundation Grant
foundation grant
Accepting applications
Apply

HealthWell Foundation — Pompe disease

HealthWell Foundation

Pompe disease

Verified 32d ago
Foundation Grant
foundation grant
Accepting applications
Apply

POMBILITI ATGA

AMICUS THERAPEUTICS US, LLC

POMBILITI ATGA — Contact AMICUS THERAPEUTICS US, LLC

Unverified — confirm before calling
Patient Assistance
Manufacturer Program
Accepting applications

Lumizyme

Sanofi

Verified 24d ago
copay card
Copay CardPatient Assistance
Accepting applications
Copay Card Apply

Nexviazyme

Sanofi

Pompe disease

Verified 23d ago
copay card
Copay CardPatient Assistance
Accepting applications
Copay Card Apply

Travel grants (8)

More about Pompe disease