Clinical trials for Phelan-McDermid syndrome
4 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPhase 3NCT07281079A Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid SyndromeNeuren Pharmaceuticals Limited
- RECRUITINGN/ANCT07014020RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS)Peking University First Hospital
- RECRUITINGPHASE1, PHASE2NCT06662188JAG201 Gene Therapy Study in Children & Adults With SHANK3 HaploinsufficiencyJaguar Gene Therapy, LLC · PI: Dan Gallo, PhD
- ACTIVE NOT RECRUITINGNCT02461420Mapping the Genotype, Phenotype, and Natural History of Phelan-McDermid SyndromeBoston Children's Hospital · PI: Alexander Kolevzon, MD