Off-periods in Parkinson disease not responding to oral treatment

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Overview

Off-periods in Parkinson disease refer to times when the medications used to control Parkinson symptoms stop working effectively, causing a return of symptoms like tremor, stiffness, slowness of movement, and difficulty walking. In Parkinson disease, the brain gradually loses cells that produce dopamine, a chemical messenger important for smooth, coordinated movement. Medications like levodopa help replace dopamine, but over time — often after several years of treatment — the effect of each dose may wear off before the next dose is due, or the medication may kick in unpredictably. These are called 'off-periods' or 'motor fluctuations.' This specific condition focuses on off-periods that do not respond well to adjustments in oral medications, meaning that changing the dose, timing, or type of pills taken by mouth has not been enough to control these episodes. During off-periods, patients may experience sudden freezing, severe tremor, muscle rigidity, anxiety, sweating, and difficulty speaking or swallowing. The treatment landscape for refractory off-periods has expanded significantly in recent years. Options now include non-oral rescue therapies such as subcutaneous apomorphine injections, inhaled levodopa, sublingual apomorphine films, continuous subcutaneous apomorphine infusion pumps, and intestinal gel infusions of levodopa-carbidopa. Deep brain stimulation surgery is another option for eligible patients. These approaches bypass the digestive system, which can be unreliable in advanced Parkinson disease.

Key symptoms:

Sudden return of tremor or shakingMuscle stiffness and rigiditySlowness of movement or feeling frozen in placeDifficulty walking or shuffling gaitTrouble speaking or slurred speechDifficulty swallowingAnxiety or panic during off-periodsSweating or feeling overheatedPain or cramping in musclesMood changes including depression or irritabilityFatigue and low energyUnpredictable switching between good and bad periodsDifficulty with fine motor tasks like buttoning clothesBalance problems and risk of falling

Inheritance

Multifactorial

Caused by a mix of several genes and environmental factors

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

1 event
Dec 2002

Extraneal (with 7.5% Icodextrin) Peritoneal Dialysis Solutio: FDA approved

For use as a single daily exchange for the long (8-16 hour) dwell during continuous ambulatory peritoneal dialysis (CAPD) or automated peritoneal dialysis (APD) for the management of chronic renal failure.

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

2 available

Livtencity

maribavir· Takeda Pharmaceuticals U.S.A., Inc.
LIVTENCITY is indicated for the treatment of adults and pediatric patients (12 years of age and older and weighing at least 35 kg) with post-transplant cytomegalovirus (CMV) infection/disease that is

LIVTENCITY is indicated for the treatment of adults and pediatric patients (12 years of age and older and weighing at least 35 kg) with post-transplant cytomegalovirus (CMV) infection/disease that is refractory to treatment (with or without genotypic resistance) with ganciclovir, valganciclovir, cidofovir or foscarnet

Extraneal (with 7.5% Icodextrin) Peritoneal Dialysis Solutio

Icodextrin 7.5% with Electrolytes Peritoneal Dialysis Solution· Baxter Healthcare CorporationOrphan Drug
For use as a single daily exchange for the long (8-16 hour) dwell during continuous ambulatory peritoneal dialysis (CAPD) or automated peritoneal dialysis (APD) for the management of chronic renal fai

For use as a single daily exchange for the long (8-16 hour) dwell during continuous ambulatory peritoneal dialysis (CAPD) or automated peritoneal dialysis (APD) for the management of chronic renal failure.

No actively recruiting trials found for Off-periods in Parkinson disease not responding to oral treatment at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Off-periods in Parkinson disease not responding to oral treatment community →

No specialists are currently listed for Off-periods in Parkinson disease not responding to oral treatment.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

1 resources
Livtencity(maribavir)Takeda Pharmaceuticals U.S.A., Inc.

Travel Grants

No travel grants are currently matched to Off-periods in Parkinson disease not responding to oral treatment.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Off-periods in Parkinson disease not responding to oral treatment

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What non-oral treatment options are available for my off-periods, and which would you recommend for me?,Am I a candidate for deep brain stimulation surgery?,How can I better track my on and off times to help guide treatment decisions?,Are there any clinical trials for new treatments for refractory off-periods that I could participate in?,What should my caregiver do if I have a severe off-period and cannot move or swallow?,Could my current medications be contributing to the unpredictability of my off-periods?,What support services — physical therapy, occupational therapy, mental health support — do you recommend?

Common questions about Off-periods in Parkinson disease not responding to oral treatment

What is Off-periods in Parkinson disease not responding to oral treatment?

Off-periods in Parkinson disease refer to times when the medications used to control Parkinson symptoms stop working effectively, causing a return of symptoms like tremor, stiffness, slowness of movement, and difficulty walking. In Parkinson disease, the brain gradually loses cells that produce dopamine, a chemical messenger important for smooth, coordinated movement. Medications like levodopa help replace dopamine, but over time — often after several years of treatment — the effect of each dose may wear off before the next dose is due, or the medication may kick in unpredictably. These are ca

How is Off-periods in Parkinson disease not responding to oral treatment inherited?

Off-periods in Parkinson disease not responding to oral treatment follows a multifactorial inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Off-periods in Parkinson disease not responding to oral treatment typically begin?

Typical onset of Off-periods in Parkinson disease not responding to oral treatment is adult. Age of onset can vary across affected individuals.

What treatment and support options exist for Off-periods in Parkinson disease not responding to oral treatment?

1 patient support program are currently tracked on UniteRare for Off-periods in Parkinson disease not responding to oral treatment. See the treatments and support programs sections for copay assistance, eligibility, and contact details.