OBSOLETE: Syndrome associated with Pierre Robin syndrome

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:138063
Who is this for?
Show terms as
1FDA treatments8Treatment centers1Financial resources

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

This Orphanet entry (code 138063) is labeled as 'OBSOLETE: Syndrome associated with Pierre Robin syndrome,' meaning it is no longer an active or recognized classification in the Orphanet rare disease database. It was previously used as a grouping term for conditions that occur alongside Pierre Robin sequence (also called Pierre Robin syndrome). Pierre Robin sequence itself is a condition present at birth that involves three main features: a very small lower jaw (micrognathia), a tongue that falls back into the throat (glossoptosis), and often a gap in the roof of the mouth (cleft palate). These features can cause serious breathing and feeding difficulties in newborns. Because Pierre Robin sequence can appear as part of many different genetic syndromes — such as Stickler syndrome, Treacher Collins syndrome, velocardiofacial syndrome (22q11.2 deletion syndrome), and others — this obsolete grouping was once used to capture those overlapping conditions. Since this code is no longer in use, patients and families who were previously classified under this term should work with their clinical genetics team to identify the specific underlying syndrome causing their Pierre Robin features. Proper diagnosis of the specific syndrome is essential because each condition has its own genetic cause, inheritance pattern, prognosis, and management plan. Treatment for Pierre Robin sequence generally focuses on securing the airway, supporting feeding, and surgically repairing the cleft palate when present.

Also known as:

Key symptoms:

Very small or recessed lower jawTongue falling back into the throat causing airway blockageOpening or gap in the roof of the mouth (cleft palate)Difficulty breathing, especially when lying on the backFeeding difficulties and poor weight gainNoisy breathing or snoring in infancyEpisodes of choking or turning blueEar infectionsHearing problemsSpeech difficultiesFacial differences depending on the underlying syndromePossible eye problems such as nearsightednessPossible joint or skeletal abnormalitiesPossible heart defects depending on the specific syndrome

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

FDA & Trial Timeline

3 events
Dec 2020

HETLIOZ: FDA approved

Treatment of nighttime sleep disturbances in Smith-Magenis Syndrome (SMS) in patients 16 years of age and older

FDAcompleted
Apr 2004

Chirostim: FDA approved

Stimulation of pancreatic secretions, including bicarbonate, to aid in the diagnosis of pancreatic exocrine dysfunction, stimulation of gastrin secretion to aid in the diagnosis of gastrinoma, and stimulation of pancreatic secretions to facilitate the identification of the ampulla of Vater and accessory papilla during endoscopic retrograde cholangiopancreatography

FDAcompleted
Apr 2002

Secreflo: FDA approved

Use in secretin stimulation testing for stimulation of gastrin secretion to aid in the diagnosis of gastrinoma

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

Secreflo

Synthetic porcine secretin· ChiRhoClin, Inc.Orphan Drug

Use in secretin stimulation testing for stimulation of gastrin secretion to aid in the diagnosis of gastrinoma

No actively recruiting trials found for OBSOLETE: Syndrome associated with Pierre Robin syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the OBSOLETE: Syndrome associated with Pierre Robin syndrome community →

No specialists are currently listed for OBSOLETE: Syndrome associated with Pierre Robin syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

1 resources

HETLIOZ

Vanda Pharmaceuticals, Inc.

Unverified — confirm before calling
copay card
copay assistancePatient Assistance
Accepting applications

Travel Grants

No travel grants are currently matched to OBSOLETE: Syndrome associated with Pierre Robin syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open OBSOLETE: Syndrome associated with Pierre Robin syndromeForum →

No community posts yet. Be the first to share your experience with OBSOLETE: Syndrome associated with Pierre Robin syndrome.

Start the conversation →

Latest news about OBSOLETE: Syndrome associated with Pierre Robin syndrome

No recent news articles for OBSOLETE: Syndrome associated with Pierre Robin syndrome.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Has a specific genetic syndrome been identified as the cause of my child's Pierre Robin sequence?,What genetic testing do you recommend to find the underlying cause?,How severe is my child's airway obstruction, and what treatment approach do you recommend?,What feeding strategies or devices should we use, and should we see a feeding specialist?,When will cleft palate repair surgery be recommended, and what should we expect?,What other specialists should my child see regularly (hearing, vision, heart)?,Are there any clinical trials or new treatments we should know about?

Common questions about OBSOLETE: Syndrome associated with Pierre Robin syndrome

What is OBSOLETE: Syndrome associated with Pierre Robin syndrome?

This Orphanet entry (code 138063) is labeled as 'OBSOLETE: Syndrome associated with Pierre Robin syndrome,' meaning it is no longer an active or recognized classification in the Orphanet rare disease database. It was previously used as a grouping term for conditions that occur alongside Pierre Robin sequence (also called Pierre Robin syndrome). Pierre Robin sequence itself is a condition present at birth that involves three main features: a very small lower jaw (micrognathia), a tongue that falls back into the throat (glossoptosis), and often a gap in the roof of the mouth (cleft palate). Thes

At what age does OBSOLETE: Syndrome associated with Pierre Robin syndrome typically begin?

Typical onset of OBSOLETE: Syndrome associated with Pierre Robin syndrome is neonatal. Age of onset can vary across affected individuals.

What treatment and support options exist for OBSOLETE: Syndrome associated with Pierre Robin syndrome?

3 patient support programs are currently tracked on UniteRare for OBSOLETE: Syndrome associated with Pierre Robin syndrome. See the treatments and support programs sections for copay assistance, eligibility, and contact details.