OBSOLETE: Heckenlively syndrome

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ORPHA:2120
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Overview

Heckenlively syndrome is an extremely rare condition that has been described in the medical literature but is now considered an obsolete diagnostic term, meaning it is no longer used as a separate disease classification by most experts. The condition was originally described as a combination of eye problems, specifically retinitis pigmentosa (a progressive loss of vision due to degeneration of the retina), along with skeletal abnormalities and other features. Patients with this condition were noted to have progressive vision loss, particularly difficulty seeing in dim light (night blindness), narrowing of the visual field (tunnel vision), and bone or joint abnormalities. Because this syndrome is now considered obsolete, patients who were previously diagnosed with Heckenlively syndrome may have their condition reclassified under a more specific diagnosis based on modern genetic testing. The features originally grouped under this name likely overlap with other known genetic conditions affecting the eyes and skeleton. If you or a family member has been given this diagnosis, it is important to seek updated genetic evaluation to determine the most accurate current diagnosis, which can guide treatment and management decisions. Treatment has generally been supportive, focusing on managing vision loss and any skeletal issues.

Key symptoms:

Progressive vision lossNight blindness (difficulty seeing in low light)Tunnel vision (loss of side vision)Bone or joint abnormalitiesSkeletal changesSensitivity to bright lightGradual loss of central vision

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for OBSOLETE: Heckenlively syndrome.

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No actively recruiting trials found for OBSOLETE: Heckenlively syndrome at this time.

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Search ClinicalTrials.gov ↗Join the OBSOLETE: Heckenlively syndrome community →

No specialists are currently listed for OBSOLETE: Heckenlively syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to OBSOLETE: Heckenlively syndrome.

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Community

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Is my diagnosis still classified as Heckenlively syndrome, or should it be updated based on current knowledge?,Should I have genetic testing to identify the specific gene causing my condition?,Am I eligible for any gene therapy or clinical trials?,How quickly is my vision likely to change, and how often should I be monitored?,What low vision aids or rehabilitation services do you recommend?,Are there any supplements or medications that could slow my vision loss?,Should my family members be tested for this condition?

Common questions about OBSOLETE: Heckenlively syndrome

What is OBSOLETE: Heckenlively syndrome?

Heckenlively syndrome is an extremely rare condition that has been described in the medical literature but is now considered an obsolete diagnostic term, meaning it is no longer used as a separate disease classification by most experts. The condition was originally described as a combination of eye problems, specifically retinitis pigmentosa (a progressive loss of vision due to degeneration of the retina), along with skeletal abnormalities and other features. Patients with this condition were noted to have progressive vision loss, particularly difficulty seeing in dim light (night blindness),