OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency

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Overview

Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency is a very rare and severe heart condition that affects babies, typically appearing in the first months of life. Note that this disease entry has been marked as 'obsolete' in medical databases, meaning it has been reclassified or merged into broader categories of mitochondrial complex I deficiency disorders. In this condition, the heart muscle becomes abnormally thick (hypertrophic cardiomyopathy), which makes it harder for the heart to pump blood effectively. The root cause is a problem with complex I, which is a key part of the energy-producing machinery inside cells called mitochondria. When complex I does not work properly, cells — especially those in energy-demanding organs like the heart — cannot make enough energy to function normally. Babies with this condition typically develop signs of heart failure early in life, including difficulty breathing, poor feeding, and failure to thrive. The disease progresses rapidly and is unfortunately associated with a very poor outcome. Treatment is mainly supportive, focusing on managing heart failure symptoms and providing nutritional support. There are currently no curative treatments available, though research into mitochondrial diseases continues to advance.

Also known as:

Key symptoms:

Thickened heart muscle (hypertrophic cardiomyopathy)Difficulty breathingPoor feedingFailure to gain weight and growExtreme tiredness and low energyRapid heartbeatBluish skin color (cyanosis)Swelling in the legs or abdomenLow muscle tone (floppiness)Lactic acidosis (buildup of acid in the blood)Liver problemsDevelopmental delays

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency.

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No actively recruiting trials found for OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency at this time.

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No specialists are currently listed for OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency.

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Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.What is the specific genetic cause of my baby's condition, and does it affect how the disease might progress?,Are there any supplements or medications that might help support my baby's heart or mitochondrial function?,What signs should I watch for that would mean I need to bring my baby to the emergency room?,Are there any clinical trials or experimental treatments available for this condition?,What palliative care and family support services are available to us?,What does this diagnosis mean for future pregnancies — what are the chances of having another affected child?,Can you refer us to a center that specializes in mitochondrial diseases?

Common questions about OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency

What is OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency?

Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency is a very rare and severe heart condition that affects babies, typically appearing in the first months of life. Note that this disease entry has been marked as 'obsolete' in medical databases, meaning it has been reclassified or merged into broader categories of mitochondrial complex I deficiency disorders. In this condition, the heart muscle becomes abnormally thick (hypertrophic cardiomyopathy), which makes it harder for the heart to pump blood effectively. The root cause is a problem with complex I, which

At what age does OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency typically begin?

Typical onset of OBSOLETE: Fatal infantile hypertrophic cardiomyopathy due to mitochondrial complex I deficiency is infantile. Age of onset can vary across affected individuals.