OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance

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ORPHA:306486
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Overview

This Orphanet entry (code 306486) is labeled as OBSOLETE, meaning it is no longer considered a valid or active disease classification. The original concept referred to 'Congenital sucrase-isomaltase deficiency without sucrose intolerance,' which described a situation where a person was born with reduced or absent sucrase-isomaltase enzyme activity but did not show the typical symptoms of sugar (sucrose) intolerance, such as diarrhea, bloating, and abdominal pain after eating table sugar or starchy foods. Sucrase-isomaltase is an enzyme found in the lining of the small intestine that helps break down certain sugars and starches. This classification was retired because the medical community determined it did not represent a distinct clinical condition warranting its own disease entry. Individuals who carry genetic variants in the sucrase-isomaltase gene (SI gene) but do not have symptoms are now generally considered carriers or individuals with subclinical enzyme variation rather than having a separate disease. The active and recognized condition is Congenital Sucrase-Isomaltase Deficiency (CSID), which involves actual symptoms of sugar malabsorption. If you or a family member has been given this diagnosis or a related one, it is recommended to speak with a gastroenterologist or clinical geneticist to clarify the current diagnostic classification and whether any follow-up is needed.

Also known as:

Key symptoms:

Bloating and gas after eating sugary or starchy foodsWatery diarrhea after mealsStomach cramps or painNausea after eatingPoor weight gain or failure to thrive in infantsIrritability in babies after feedingFeeling full or uncomfortable quickly after eatingLoose stools that may be frothy or acidic

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance.

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No actively recruiting trials found for OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance at this time.

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No specialists are currently listed for OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance.

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Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance.

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.This diagnosis is listed as obsolete — does my child actually have congenital sucrase-isomaltase deficiency (CSID)?,Should we pursue genetic testing of the SI gene to clarify the diagnosis?,Are there any dietary changes we should make even if there are no current symptoms?,Could symptoms develop later in life, and what should we watch for?,Is enzyme replacement therapy (Sucraid) needed in our case?,Should other family members be tested for SI gene variants?,Can you refer us to a dietitian experienced with carbohydrate malabsorption?

Common questions about OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance

What is OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance?

This Orphanet entry (code 306486) is labeled as OBSOLETE, meaning it is no longer considered a valid or active disease classification. The original concept referred to 'Congenital sucrase-isomaltase deficiency without sucrose intolerance,' which described a situation where a person was born with reduced or absent sucrase-isomaltase enzyme activity but did not show the typical symptoms of sugar (sucrose) intolerance, such as diarrhea, bloating, and abdominal pain after eating table sugar or starchy foods. Sucrase-isomaltase is an enzyme found in the lining of the small intestine that helps brea

How is OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance inherited?

OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance typically begin?

Typical onset of OBSOLETE: Congenital sucrase-isomaltase deficiency without sucrose intolerance is infantile. Age of onset can vary across affected individuals.