OBSOLETE: Congenital ichthyosis with trichothiodystrophy

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Overview

Congenital ichthyosis with trichothiodystrophy (TTD) is a rare genetic skin and hair disorder that is present from birth. This condition has been reclassified (marked as 'obsolete' in some databases) because it is now grouped under the broader category of trichothiodystrophy syndromes. The disease affects the skin and hair due to problems with sulfur-rich proteins. People with this condition are born with dry, thick, scaly skin (called ichthyosis) along with brittle, fragile hair that breaks easily. When examined under a special microscope with polarized light, the hair shows a characteristic 'tiger tail' banding pattern, which is a hallmark of trichothiodystrophy. The underlying cause involves mutations in genes responsible for DNA repair and transcription, most commonly the ERCC2 (XPD) and ERCC3 (XPB) genes. Because these genes play important roles beyond just skin and hair, some patients may also experience growth problems, intellectual disability, sensitivity to sunlight, and recurrent infections. The severity varies widely from person to person. There is currently no cure for this condition. Treatment focuses on managing symptoms, including regular use of moisturizers and emollients for the skin, gentle hair care to minimize breakage, and monitoring for any associated complications such as infections or developmental delays. A team of specialists is usually needed to provide comprehensive care.

Key symptoms:

Dry, thick, scaly skin present from birthBrittle hair that breaks easilyShort, sparse hairTiger tail pattern of hair under polarized light microscopySensitivity to sunlight in some casesShort stature or poor growthIntellectual disability or developmental delays in some casesRecurrent infectionsAbnormal nails that are brittle or ridgedLow birth weightReduced fertility in some casesDry, red, or irritated skin

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for OBSOLETE: Congenital ichthyosis with trichothiodystrophy.

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No actively recruiting trials found for OBSOLETE: Congenital ichthyosis with trichothiodystrophy at this time.

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No specialists are currently listed for OBSOLETE: Congenital ichthyosis with trichothiodystrophy.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to OBSOLETE: Congenital ichthyosis with trichothiodystrophy.

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.How severe is my child's condition, and which body systems are affected?,What is the specific genetic mutation, and what does it mean for my child's outlook?,What skin care products and routines do you recommend?,Should my child avoid sun exposure, and if so, what precautions should we take?,Are there developmental assessments or therapies my child should start now?,What signs of infection should I watch for, and when should I seek emergency care?,Are there any clinical trials or new treatments being studied for this condition?

Common questions about OBSOLETE: Congenital ichthyosis with trichothiodystrophy

What is OBSOLETE: Congenital ichthyosis with trichothiodystrophy?

Congenital ichthyosis with trichothiodystrophy (TTD) is a rare genetic skin and hair disorder that is present from birth. This condition has been reclassified (marked as 'obsolete' in some databases) because it is now grouped under the broader category of trichothiodystrophy syndromes. The disease affects the skin and hair due to problems with sulfur-rich proteins. People with this condition are born with dry, thick, scaly skin (called ichthyosis) along with brittle, fragile hair that breaks easily. When examined under a special microscope with polarized light, the hair shows a characteristic

How is OBSOLETE: Congenital ichthyosis with trichothiodystrophy inherited?

OBSOLETE: Congenital ichthyosis with trichothiodystrophy follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does OBSOLETE: Congenital ichthyosis with trichothiodystrophy typically begin?

Typical onset of OBSOLETE: Congenital ichthyosis with trichothiodystrophy is neonatal. Age of onset can vary across affected individuals.