OBSOLETE: Anemia due to adenosine triphosphatase deficiency

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Overview

Anemia due to adenosine triphosphatase (ATPase) deficiency is an extremely rare inherited blood disorder that has been described in medical literature but is now considered an obsolete diagnostic category. This condition was originally characterized by a deficiency of ATPase enzymes in red blood cells, which led to the premature destruction of these cells (a process called hemolysis), resulting in hemolytic anemia. Red blood cells need ATPase enzymes to maintain their shape, flexibility, and ability to carry oxygen throughout the body. When these enzymes are lacking or not working properly, red blood cells become fragile and break down faster than the body can replace them. Patients with this condition may experience symptoms typical of hemolytic anemia, including fatigue, pale skin, shortness of breath, jaundice (yellowing of the skin and eyes), and an enlarged spleen. The severity can vary from mild to more significant anemia requiring medical attention. This diagnosis has been reclassified as obsolete in modern medical databases, meaning that cases previously labeled under this condition are now more precisely categorized under other red blood cell enzyme deficiency disorders. Advances in genetic testing and enzyme analysis have allowed doctors to identify the specific enzyme defects more accurately. Treatment has generally been supportive, focusing on managing anemia symptoms, and may include blood transfusions in severe cases, folic acid supplementation, and monitoring for complications related to chronic hemolysis.

Key symptoms:

Fatigue and low energyPale skinYellowing of the skin and eyes (jaundice)Shortness of breathRapid heartbeatEnlarged spleenDark-colored urineDizziness or lightheadednessWeaknessGallstones at a young age

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for OBSOLETE: Anemia due to adenosine triphosphatase deficiency.

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No specialists are currently listed for OBSOLETE: Anemia due to adenosine triphosphatase deficiency.

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Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.What is the exact cause of my anemia, and can genetic testing help clarify the diagnosis?,How severe is my condition, and how often will I need blood tests?,Will I or my child need blood transfusions, and if so, how often?,Should I take folic acid or any other supplements?,Are there activities or medications I should avoid that could worsen the anemia?,Is splenectomy something that might help in my case?,What are the chances of passing this condition to my children?

Common questions about OBSOLETE: Anemia due to adenosine triphosphatase deficiency

What is OBSOLETE: Anemia due to adenosine triphosphatase deficiency?

Anemia due to adenosine triphosphatase (ATPase) deficiency is an extremely rare inherited blood disorder that has been described in medical literature but is now considered an obsolete diagnostic category. This condition was originally characterized by a deficiency of ATPase enzymes in red blood cells, which led to the premature destruction of these cells (a process called hemolysis), resulting in hemolytic anemia. Red blood cells need ATPase enzymes to maintain their shape, flexibility, and ability to carry oxygen throughout the body. When these enzymes are lacking or not working properly, re

How is OBSOLETE: Anemia due to adenosine triphosphatase deficiency inherited?

OBSOLETE: Anemia due to adenosine triphosphatase deficiency follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.