Non-syndromic longitudinal limb defect

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Overview

Non-syndromic longitudinal limb defect is a rare congenital condition where one or more limbs — arms or legs — are partially or completely missing along their length at birth. Unlike syndromic limb defects, this condition occurs on its own, without other major birth defects or intellectual disabilities as part of a recognized syndrome. The term 'longitudinal' means the missing or underdeveloped bone or tissue runs along the long axis of the limb — for example, a missing radius bone in the forearm, or an absent fibula in the lower leg. Common examples include radial ray deficiency (missing or small radius), fibular hemimelia (absent or short fibula), and tibial hemimelia (absent tibia). Children born with this condition may have a limb that looks shorter than usual, has missing fingers or toes, or is shaped differently. The affected limb may have limited movement or function depending on which bones are involved. Some children adapt remarkably well, while others may benefit from prosthetics, surgery, or physical therapy to improve function and independence. Treatment is tailored to each person and may include prosthetic limbs, orthopedic surgery to lengthen or reconstruct bones, and physical or occupational therapy. The goal is to maximize function and quality of life. With the right support, many people with this condition live full, active lives.

Key symptoms:

Missing or underdeveloped bone in an arm or legShorter than normal arm or legMissing, fused, or extra fingers or toes on the affected limbUnusual shape or appearance of the hand, foot, forearm, or lower legLimited range of motion in the affected limbDifficulty gripping objects if the hand or forearm is affectedDifficulty walking or bearing weight if the leg is affectedInstability of joints near the defectCurved or bowed appearance of the limb

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Non-syndromic longitudinal limb defect.

View clinical trials →

No actively recruiting trials found for Non-syndromic longitudinal limb defect at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Non-syndromic longitudinal limb defect community →

No specialists are currently listed for Non-syndromic longitudinal limb defect.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Non-syndromic longitudinal limb defect.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Non-syndromic longitudinal limb defect

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which specific bones are affected and what does that mean for my child's function?,Should we pursue genetic testing to understand the cause?,When is the right time to start using a prosthetic limb?,What surgical options are available and what are the risks and benefits?,How often will my child need new prosthetics as they grow?,What therapy services should we start and how often?,Are there support groups or other families we can connect with?

Common questions about Non-syndromic longitudinal limb defect

What is Non-syndromic longitudinal limb defect?

Non-syndromic longitudinal limb defect is a rare congenital condition where one or more limbs — arms or legs — are partially or completely missing along their length at birth. Unlike syndromic limb defects, this condition occurs on its own, without other major birth defects or intellectual disabilities as part of a recognized syndrome. The term 'longitudinal' means the missing or underdeveloped bone or tissue runs along the long axis of the limb — for example, a missing radius bone in the forearm, or an absent fibula in the lower leg. Common examples include radial ray deficiency (missing or s

At what age does Non-syndromic longitudinal limb defect typically begin?

Typical onset of Non-syndromic longitudinal limb defect is neonatal. Age of onset can vary across affected individuals.