Clinical trials for Myotonic dystrophy
21 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPhase 3NCT07486934Efficacy, Safety, and Tolerability of DYNE-101 in Participants With Myotonic Dystrophy Type 1Dyne Therapeutics
- RECRUITINGPhase 2NCT07220603An Open-Label Extension Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1 (FREEDOM-OLE)PepGen Inc
- ACTIVE NOT RECRUITINGNCT07493525Fall Frequency and Factors Affecting Dynamic Balance in Patients With Myotonic Dystrophy Type 1Antalya Training and Research Hospital · PI: Hanife Hale Hekim, MD
- RECRUITINGNCT06747884Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy ExtensionVirginia Commonwealth University · PI: Nicholas Johnson, MD, MSCI, FAAN
- RECRUITINGNCT07385443The Spanish National Registry for Myotonic Dystrophy Type 1Fundació Institut Germans Trias i Pujol · PI: Gisela Nogales Gadea, Ph.D.
- RECRUITINGNCT07362875Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic DystrophyWake Forest University Health Sciences · PI: Araya Puwanant, MD
- RECRUITINGN/ANCT06809049Music Intervention for Brain-Heart Disease in Myotonic Dystrophy Type 1 (DM1)Hanns Lochmuller
- RECRUITINGPhase 2NCT06667453A Clinical Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1PepGen Inc
- RECRUITINGPhase 3NCT05532813Evaluation of the Efficacy and Safety of Metformin in the Myotonic Dystrophy Type 1 (Steinert's Disease)Assistance Publique - Hôpitaux de Paris · PI: Pascal LAFORÊT, MD, PhD
- RECRUITINGPHASE1, PHASE2NCT06300307Study of ATX-01 in Participants With DM1ARTHEx Biotech S.L.
- RECRUITINGN/ANCT06316778Pelvic Floor Muscle Training for Women with Myotonic DystrophyUniversité de Sherbrooke
- RECRUITINGPHASE1, PHASE2NCT06138743Study of ARO-DM1 in Subjects With Type 1 Myotonic DystrophyArrowhead Pharmaceuticals
- RECRUITINGNCT06378216Myotonic Dystrophy Type 1 Congenital and Juvenile Form: From Diagnosis to Rehabilitation [MDCJ-NeuBeRe]IRCCS Eugenio Medea
- RECRUITINGNCT05224778DMCRN-02-001: Assessing Pediatric Endpoints in DM1Virginia Commonwealth University · PI: Nicholas E. Johnson, MD
- ACTIVE NOT RECRUITINGNCT04656210Myotonic Dystrophy - Vascular and CognitionUniversity Hospital, Lille · PI: Céline TARD, MD
- RECRUITINGPHASE2, PHASE3NCT05004129Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic DystrophyAMO Pharma Limited · PI: Harriet Gray-Stephens, BM BCh, MA (Oxon), MFPM
- ACTIVE NOT RECRUITINGN/ANCT05072288A Remote Physical Activity Program in the Population Suffering from Type 1 Myotonic DystrophyUniversité du Québec à Chicoutimi · PI: Elise Duchesne
- ENROLLING BY INVITATIONNCT06101940A Multicenter Phenotype-Genotype Analysis of DM1 Patients in ChinaHuashan Hospital · PI: Chongbo Zhao, PhD
- ACTIVE NOT RECRUITINGNCT04616807An Observational Study in Adult Patients With Non-dystrophic Myotonic DisordersLupin Ltd.
- RECRUITINGNCT05020002Extracellular RNA Biomarkers of Myotonic DystrophyMassachusetts General Hospital · PI: Thurman M. Wheeler, MD
- RECRUITINGNCT03981575Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)Virginia Commonwealth University · PI: Nicholas Johnson, MD