Multisystem inflammatory syndrome in children and adults

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:598363U10.9
Who is this for?
Show terms as
3FDA treatments1Specialists8Treatment centers1Financial resources

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Also known as:

Orphanet ↗NORD ↗

FDA & Trial Timeline

4 events
Apr 2023

COAGADEX: FDA approved

in adults and children with hereditary Factor X deficiency for routine prophylaxis to reduce the frequency of bleeding episodes; on-demand treatment and control of bleeding episodes; and perioperative management of bleeding in patients with mild, moderate, and severe hereditary Factor X deficiency

FDAcompleted
Feb 2023

ALTUVIIIO: FDA approved

in adults and children with hemophilia A (congenital factor VIII deficiency) for routine prophylaxis to reduce the frequency of bleeding episodes; on-demand treatment and control of bleeding episodes; and perioperative management of bleeding

FDAcompleted
Nov 2022A Study to Learn About The COVID-19 (Study) Vaccine (Called COMIRNATY) in People That Are Less Than 21 Years Old.

Pfizer — PHASE4

TrialRECRUITING
Mar 2014

ALPROLIX: FDA approved

Adults and children with Hemophilia B for control and prevention of bleeding episodes, perioperative management, and routine prophylaxis to prevent or reduce the frequency of bleeding episodes.

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

3 available

COAGADEX

Coagulation factor X (human)· Bio Products Laboratory LimitedOrphan Drug
in adults and children with hereditary Factor X deficiency for routine prophylaxis to reduce the frequency of bleeding episodes; on-demand treatment and control of bleeding episodes; and perioperative

in adults and children with hereditary Factor X deficiency for routine prophylaxis to reduce the frequency of bleeding episodes; on-demand treatment and control of bleeding episodes; and perioperative management of bleeding in patients with mild, moderate, and severe hereditary Factor X deficiency

ALTUVIIIO

ANTIHEMOPHILIC FACTOR (RECOMBINANT), FC-VWF-XTEN FUSION PROTEIN-EHTL· Bioverativ Therapeutics Inc.Orphan Drug
in adults and children with hemophilia A (congenital factor VIII deficiency) for routine prophylaxis to reduce the frequency of bleeding episodes; on-demand treatment and control of bleeding episodes;

in adults and children with hemophilia A (congenital factor VIII deficiency) for routine prophylaxis to reduce the frequency of bleeding episodes; on-demand treatment and control of bleeding episodes; and perioperative management of bleeding

ALPROLIX

Coagulation factor IX (recombinant), Fc fusion protein· Bioverativ Therapeutics, Inc.Orphan Drug

Adults and children with Hemophilia B for control and prevention of bleeding episodes, perioperative management, and routine prophylaxis to prevent or reduce the frequency of bleeding episodes.

No actively recruiting trials found for Multisystem inflammatory syndrome in children and adults at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Multisystem inflammatory syndrome in children and adults community →

Specialists

1 foundView all specialists →
TB
Thomas Waterfield, BMBCh
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

1 resources
ALTUVIIIO(ANTIHEMOPHILIC FACTOR (RECOMBINANT), FC-VWF-XTEN FUSION PROTEIN-EHTL)Bioverativ Therapeutics Inc.

Travel Grants

No travel grants are currently matched to Multisystem inflammatory syndrome in children and adults.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Multisystem inflammatory syndrome in children and adultsForum →

No community posts yet. Be the first to share your experience with Multisystem inflammatory syndrome in children and adults.

Start the conversation →

Latest news about Multisystem inflammatory syndrome in children and adults

Disease timeline:

New recruiting trial: A Study to Learn About The COVID-19 (Study) Vaccine (Called COMIRNATY) in People That Are Less Than 21 Years Old.

A new clinical trial is recruiting patients for Multisystem inflammatory syndrome in children and adults

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Multisystem inflammatory syndrome in children and adults

Which specialists treat Multisystem inflammatory syndrome in children and adults?

1 specialists and care centers treating Multisystem inflammatory syndrome in children and adults are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Multisystem inflammatory syndrome in children and adults?

1 patient support program are currently tracked on UniteRare for Multisystem inflammatory syndrome in children and adults. See the treatments and support programs sections for copay assistance, eligibility, and contact details.