Specialists for Mucopolysaccharidosis type 4A
6 physicians and care centers identified from ClinicalTrials.gov trial PIs, PubMed publications, and the NPPES NPI registry.
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Specialists are identified from ClinicalTrials.gov principal investigators, PubMed publications, and the NPI registry, then ranked through an automated scoring pipeline.
Report missing data- Debra LounsburyRare Disease / Clinical ResearchBioMarin PharmaceuticalPI×5 1
- Tippi MacKenzie, MDRare Disease SpecialistUniversity of California, San FranciscoSan Francisco, CaliforniaPI×2
- Celeste Decker, MDRare Disease / Clinical ResearchBioMarin Pharmceutical Inc.CONCORD, NHPI×5
- Shunji Tomatsu, MD PhDRare Disease / Clinical ResearchNemours Children's CarePI×1
- Ellen B Fung, PhD, PhD, RDRare Disease / Clinical ResearchUniversity of California, San FranciscoOAKLAND, CAPI×1
- Richard Curtis Rogers, MDRare Disease / Clinical ResearchGreenwood Genetic CenterPI×1