Larsen-like osseous dysplasia-short stature syndrome

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:2370OMIM:608545Q74.8
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Larsen-like osseous dysplasia-short stature syndrome is an extremely rare genetic bone disorder that shares some features with classic Larsen syndrome but has its own distinct characteristics. The condition primarily affects how bones and joints develop, leading to noticeable short stature and skeletal abnormalities. People with this syndrome may have joint dislocations (where bones slip out of their normal position at a joint), unusual facial features, and abnormal development of the bones in the spine, limbs, and other parts of the skeleton. The term 'osseous dysplasia' refers to abnormal bone growth and formation. Key symptoms can include short stature that becomes apparent in childhood, loose or overly flexible joints, flat facial features, and various bone shape abnormalities visible on X-rays. Some individuals may also experience problems with their airways or breathing due to abnormalities in the cartilage that supports the windpipe. Because this condition is so rare, there is no specific cure or targeted treatment. Management focuses on addressing individual symptoms as they arise. This may include orthopedic interventions such as bracing or surgery for joint dislocations and skeletal deformities, physical therapy to strengthen muscles around unstable joints, and monitoring of growth and development. A team of specialists working together is usually needed to provide the best care for affected individuals.

Key symptoms:

Short statureJoint dislocations or loose jointsFlat facial appearanceAbnormal bone shape visible on X-raysSpinal abnormalitiesShort limbs or limb length differencesBroad or flat nose bridgeDelayed motor developmentAbnormal cartilage developmentCurved spine (scoliosis or kyphosis)Unusual hand or finger shapeBreathing difficulties in some cases

Clinical phenotype terms (21)— hover any for plain English
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Larsen-like osseous dysplasia-short stature syndrome.

View clinical trials →

No actively recruiting trials found for Larsen-like osseous dysplasia-short stature syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Larsen-like osseous dysplasia-short stature syndrome community →

No specialists are currently listed for Larsen-like osseous dysplasia-short stature syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Larsen-like osseous dysplasia-short stature syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Larsen-like osseous dysplasia-short stature syndromeForum →

No community posts yet. Be the first to share your experience with Larsen-like osseous dysplasia-short stature syndrome.

Start the conversation →

Latest news about Larsen-like osseous dysplasia-short stature syndrome

No recent news articles for Larsen-like osseous dysplasia-short stature syndrome.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific skeletal abnormalities does my child have, and how might they change over time?,Should we pursue genetic testing, and what type of testing do you recommend?,What physical activities are safe, and which should be avoided to protect the joints?,How often should we schedule follow-up X-rays or other imaging?,Are there any signs of spinal instability or airway problems we should watch for at home?,What therapies (physical therapy, occupational therapy) would benefit my child most right now?,Are there any clinical trials or research studies we should know about?

Common questions about Larsen-like osseous dysplasia-short stature syndrome

What is Larsen-like osseous dysplasia-short stature syndrome?

Larsen-like osseous dysplasia-short stature syndrome is an extremely rare genetic bone disorder that shares some features with classic Larsen syndrome but has its own distinct characteristics. The condition primarily affects how bones and joints develop, leading to noticeable short stature and skeletal abnormalities. People with this syndrome may have joint dislocations (where bones slip out of their normal position at a joint), unusual facial features, and abnormal development of the bones in the spine, limbs, and other parts of the skeleton. The term 'osseous dysplasia' refers to abnormal bo

How is Larsen-like osseous dysplasia-short stature syndrome inherited?

Larsen-like osseous dysplasia-short stature syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Larsen-like osseous dysplasia-short stature syndrome typically begin?

Typical onset of Larsen-like osseous dysplasia-short stature syndrome is neonatal. Age of onset can vary across affected individuals.