Infantile glycine encephalopathy

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:289860OMIM:605899E72.5
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Infantile glycine encephalopathy, also known as the infantile form of nonketotic hyperglycinemia (NKH), is a rare inherited metabolic disorder that affects how the body breaks down the amino acid glycine. Glycine is a building block of proteins and also acts as a chemical messenger in the brain. In this condition, the glycine cleavage system — a group of enzymes responsible for breaking down glycine — does not work properly. This causes glycine to build up to dangerously high levels in the brain and body fluids. Babies with the infantile form typically appear normal at birth but begin showing symptoms within the first weeks to months of life. Common signs include extreme sleepiness (lethargy), poor muscle tone (hypotonia), difficulty feeding, seizures, and breathing problems that can include episodes where breathing stops temporarily (apnea). As the disease progresses, most affected children develop significant intellectual disability and ongoing seizure disorders that can be very difficult to control with medication. There is currently no cure for infantile glycine encephalopathy. Treatment focuses on managing symptoms, particularly controlling seizures and reducing glycine levels in the body. Sodium benzoate is commonly used to help lower glycine levels, and dextromethorphan may be used to block glycine's effects at certain brain receptors. Despite treatment, the prognosis for the infantile form remains serious, and most children experience significant developmental challenges. Early diagnosis and a coordinated care team are essential to provide the best possible quality of life.

Also known as:

Key symptoms:

Severe sleepiness or lethargyPoor muscle tone (floppy baby)Seizures that are hard to controlDifficulty feeding or poor suckingBreathing problems or pauses in breathingHiccups (often frequent and persistent)Intellectual disabilityDelayed development of motor skillsDelayed or absent speechInvoluntary jerking movements (myoclonus)Abnormal eye movementsDifficulty swallowingIrritability

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Infantile glycine encephalopathy.

View clinical trials →

No actively recruiting trials found for Infantile glycine encephalopathy at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Infantile glycine encephalopathy community →

No specialists are currently listed for Infantile glycine encephalopathy.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Infantile glycine encephalopathy.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Infantile glycine encephalopathyForum →

No community posts yet. Be the first to share your experience with Infantile glycine encephalopathy.

Start the conversation →

Latest news about Infantile glycine encephalopathy

No recent news articles for Infantile glycine encephalopathy.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific genetic mutation does my child have, and does it give any information about how severe the disease might be?,What is the best seizure management plan for my child, and what medications should we avoid?,How will we monitor glycine levels, and how often should blood and spinal fluid tests be done?,What therapies (physical, occupational, speech) should we start, and how often?,Are there any clinical trials or experimental treatments available for this condition?,What emergency plan should we have in place for seizures or breathing problems?,What support services are available for our family, including respite care and counseling?

Common questions about Infantile glycine encephalopathy

What is Infantile glycine encephalopathy?

Infantile glycine encephalopathy, also known as the infantile form of nonketotic hyperglycinemia (NKH), is a rare inherited metabolic disorder that affects how the body breaks down the amino acid glycine. Glycine is a building block of proteins and also acts as a chemical messenger in the brain. In this condition, the glycine cleavage system — a group of enzymes responsible for breaking down glycine — does not work properly. This causes glycine to build up to dangerously high levels in the brain and body fluids. Babies with the infantile form typically appear normal at birth but begin showing

How is Infantile glycine encephalopathy inherited?

Infantile glycine encephalopathy follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Infantile glycine encephalopathy typically begin?

Typical onset of Infantile glycine encephalopathy is neonatal. Age of onset can vary across affected individuals.