Imperforate oropharynx-costovertebral anomalies syndrome

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Overview

Imperforate oropharynx-costovertebral anomalies syndrome is an extremely rare condition present at birth that affects the development of the mouth, throat, ribs, and spine. The hallmark feature is an imperforate oropharynx, which means the back of the mouth and throat are blocked or sealed off, preventing normal breathing and swallowing. This is combined with costovertebral anomalies, meaning abnormalities in the ribs and the bones of the spine (vertebrae). These rib and spine defects can vary in severity and may include fused, missing, or misshapen vertebrae and ribs. Because the airway and feeding passage are blocked at birth, this condition is a medical emergency in newborns. Babies born with this syndrome typically need immediate intervention to establish an airway and allow breathing. Additional features may include other facial or skeletal abnormalities. Due to the extreme rarity of this syndrome, very few cases have been described in the medical literature, and the underlying genetic cause has not been clearly established. Treatment is primarily surgical and supportive, focusing on opening the airway, enabling feeding, and managing any associated skeletal problems. The long-term outlook depends heavily on the severity of the anomalies and how successfully they can be corrected through surgery and ongoing care.

Also known as:

Key symptoms:

Blocked or sealed-off throat (imperforate oropharynx)Inability to breathe normally at birthInability to swallow or feedAbnormally shaped or fused ribsAbnormally shaped or fused vertebrae (spine bones)Facial abnormalitiesShort neckBreathing difficultiesFailure to thrive due to feeding problemsPossible limb abnormalities

Clinical phenotype terms (27)— hover any for plain English
Abnormality of the mouthHP:0000153Abnormal lip morphologyHP:0000159Abnormality of the philtrumHP:0000288Abnormality of the pharynxHP:0000600Missing ribsHP:0000921HemivertebraeHP:0002937
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Imperforate oropharynx-costovertebral anomalies syndrome.

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No actively recruiting trials found for Imperforate oropharynx-costovertebral anomalies syndrome at this time.

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No specialists are currently listed for Imperforate oropharynx-costovertebral anomalies syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Imperforate oropharynx-costovertebral anomalies syndrome.

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.How severe is my child's airway blockage, and what is the plan to manage it?,Will my child need a tracheostomy, and if so, for how long?,What feeding method is best for my child, and will they eventually be able to eat by mouth?,How serious are the rib and spine abnormalities, and will surgery be needed?,Is genetic testing recommended, and could this condition affect future pregnancies?,What specialists should be part of my child's care team?,What is the long-term outlook for my child's development and quality of life?

Common questions about Imperforate oropharynx-costovertebral anomalies syndrome

What is Imperforate oropharynx-costovertebral anomalies syndrome?

Imperforate oropharynx-costovertebral anomalies syndrome is an extremely rare condition present at birth that affects the development of the mouth, throat, ribs, and spine. The hallmark feature is an imperforate oropharynx, which means the back of the mouth and throat are blocked or sealed off, preventing normal breathing and swallowing. This is combined with costovertebral anomalies, meaning abnormalities in the ribs and the bones of the spine (vertebrae). These rib and spine defects can vary in severity and may include fused, missing, or misshapen vertebrae and ribs. Because the airway and

How is Imperforate oropharynx-costovertebral anomalies syndrome inherited?

Imperforate oropharynx-costovertebral anomalies syndrome follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Imperforate oropharynx-costovertebral anomalies syndrome typically begin?

Typical onset of Imperforate oropharynx-costovertebral anomalies syndrome is neonatal. Age of onset can vary across affected individuals.