Immunodeficiency by defective expression of MHC class I

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:34592OMIM:604571D81.6
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Immunodeficiency by defective expression of MHC class I, also known as MHC class I deficiency or Bare Lymphocyte Syndrome type I (BLS type I), is a rare inherited immune system disorder. In this condition, the body fails to properly display a set of proteins called MHC class I molecules on the surface of most cells. These proteins act like name tags that help the immune system tell the difference between the body's own healthy cells and foreign or infected cells. Without them, a key group of immune cells called CD8+ T cells (also called cytotoxic or 'killer' T cells) cannot develop or work properly. As a result, people with this condition have a weakened immune system that struggles to fight off certain infections, especially viruses and some bacteria. The lungs are often the most affected organ, and repeated respiratory infections are the hallmark of this disease. Unlike some other immune deficiencies, this condition tends to be milder than MHC class II deficiency, and some people may not be diagnosed until later in childhood or even adulthood. Treatment focuses on preventing and managing infections, often with long-term antibiotics and antiviral medicines. In severe cases, a stem cell transplant may be considered. Regular monitoring by an immunologist is essential to protect lung health and overall quality of life.

Also known as:

Key symptoms:

Repeated lung infections (pneumonia, bronchitis)Chronic coughShortness of breathSinusitis (sinus infections)Skin infectionsSlow growth or failure to thrive in childrenFatigue and low energyEar infectionsBronchiectasis (permanent widening and scarring of the airways from repeated infections)Reduced number of CD8+ T cells in blood tests

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Immunodeficiency by defective expression of MHC class I.

View clinical trials →

No actively recruiting trials found for Immunodeficiency by defective expression of MHC class I at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Immunodeficiency by defective expression of MHC class I community →

No specialists are currently listed for Immunodeficiency by defective expression of MHC class I.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Immunodeficiency by defective expression of MHC class I.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Immunodeficiency by defective expression of MHC class IForum →

No community posts yet. Be the first to share your experience with Immunodeficiency by defective expression of MHC class I.

Start the conversation →

Latest news about Immunodeficiency by defective expression of MHC class I

No recent news articles for Immunodeficiency by defective expression of MHC class I.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which genes should be tested in my child and our family, and what do the results mean for other family members?,What infections should I be most worried about, and what are the warning signs I should act on immediately?,Should my child receive preventive antibiotics, and if so, for how long?,How often should lung function and imaging be checked to monitor for damage?,Is a stem cell transplant an option for my child, and what are the risks and benefits?,Are there any clinical trials or research studies we could participate in?,What vaccinations are safe, and which ones should be avoided?

Common questions about Immunodeficiency by defective expression of MHC class I

What is Immunodeficiency by defective expression of MHC class I?

Immunodeficiency by defective expression of MHC class I, also known as MHC class I deficiency or Bare Lymphocyte Syndrome type I (BLS type I), is a rare inherited immune system disorder. In this condition, the body fails to properly display a set of proteins called MHC class I molecules on the surface of most cells. These proteins act like name tags that help the immune system tell the difference between the body's own healthy cells and foreign or infected cells. Without them, a key group of immune cells called CD8+ T cells (also called cytotoxic or 'killer' T cells) cannot develop or work pro

How is Immunodeficiency by defective expression of MHC class I inherited?

Immunodeficiency by defective expression of MHC class I follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.