IgG4-related retroperitoneal fibrosis

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ORPHA:49041OMIM:228800K66.2
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5Active trials23Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

IgG4-related retroperitoneal fibrosis (also called IgG4-RF or IgG4-related periaortitis/periarteritis) is a rare inflammatory disease where the immune system mistakenly triggers the buildup of scar-like tissue (fibrosis) in the retroperitoneum — the space behind the abdominal cavity that contains the kidneys, major blood vessels, and the tubes that carry urine from the kidneys to the bladder (ureters). This disease belongs to a broader family of conditions called IgG4-related disease (IgG4-RD), in which a type of immune protein called IgG4 plays a central role in causing inflammation and scarring in various organs. The growing fibrous tissue can wrap around and squeeze nearby structures, most commonly the ureters, which can block urine flow and damage the kidneys. It can also press on the aorta and other major blood vessels. People with this condition often feel vague back, flank, or abdominal pain for months before a diagnosis is made. Some people have no symptoms at all until organ damage has already occurred. The good news is that IgG4-related retroperitoneal fibrosis often responds well to treatment. Corticosteroids like prednisone are the main first-line therapy and can reduce inflammation and shrink the fibrous tissue significantly. In cases where steroids alone are not enough, other immune-suppressing medications may be added. Early diagnosis and treatment are key to preventing permanent kidney damage and other complications.

Also known as:

Key symptoms:

Dull, aching pain in the lower back, flank, or abdomenSwelling or discomfort in the belly areaDecreased urine output or difficulty urinatingSwelling in the legs due to blocked lymph or blood vesselsFatigue and general feeling of being unwellHigh blood pressure (sometimes caused by kidney involvement)Unintended weight lossMild feverNauseaKidney function decline detected on blood tests

Clinical phenotype terms (43)— hover any for plain English
Increased blood urea nitrogenHP:0003138Low back painHP:0003419Large vessel vasculitisHP:0005310Unilateral renal hypoplasiaHP:0012583Anti-thyroid peroxidase antibody positivityHP:0025379Flank painHP:0030157Deep dermal perivascular inflammatory infiltrateHP:0031191Ureteropelvic junction obstructionHP:0000074Hashimoto thyroiditisHP:0000872Rheumatoid arthritisHP:0001370
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗OMIM ↗NORD ↗

FDA & Trial Timeline

5 events
Nov 2023Distinguishing Retroperitoneal Fibrosis and Sarcoma from Other Retroperitoneal Diseases Via Radiomics

Heidelberg University

TrialACTIVE NOT RECRUITING
Nov 2022Early Discontinuation of Steroid Treatment in Negative FDG-PET/CT Patients With Idiopathic Retroperitoneal Fibrosis

Assistance Publique - Hôpitaux de Paris — PHASE4

TrialRECRUITING
Mar 2020National Registry of IRPF in China

Peking Union Medical College Hospital

TrialRECRUITING
Jan 2020A Prospective Cohort Study of IRPF in China

Peking Union Medical College Hospital

TrialRECRUITING
Jul 2018Study of Sirolimus in Idiopathic Retroperitoneal Fibrosis

Peking University International Hospital — PHASE2, PHASE3

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for IgG4-related retroperitoneal fibrosis.

5 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

5 recruitingView all trials with filters →
Phase 41 trial
Early Discontinuation of Steroid Treatment in Negative FDG-PET/CT Patients With Idiopathic Retroperitoneal Fibrosis
Phase 4
Actively Recruiting
PI: Aline DECHANET (Assistance Publique - Hôpitaux de Paris (AP-HP)) · Sites: Agen, France; Brest, France +13 more · Age: 1899 yrs
Other3 trials
A Prospective Cohort Study of IRPF in China
Actively Recruiting
PI: Wen Zhang, MD (Department of Rheumatology,Peking Union Medical Co) · Sites: Beijing, Beijing Municipality · Age: 1875 yrs
Distinguishing Retroperitoneal Fibrosis and Sarcoma from Other Retroperitoneal Diseases Via Radiomics
Active
· Sites: Beijing; Mannheim, Baden-Wurttemberg
National Registry of IRPF in China
Actively Recruiting
· Sites: Beijing, Beijing Municipality · Age: 1875 yrs

Specialists

23 foundView all specialists →
YZ
Yuliya Zayats
PARK RIDGE, IL
Specialist
1 IgG4-related retroperitoneal fibrosis publication
IC
Ihor Chechotenko
Specialist
1 IgG4-related retroperitoneal fibrosis publication
DM
Dmytro Mykhailov
Specialist
1 IgG4-related retroperitoneal fibrosis publication
VK
Vladyslav Kravchenko
Specialist
1 IgG4-related retroperitoneal fibrosis publication
OI
Oleg Iaremenko
Specialist
1 IgG4-related retroperitoneal fibrosis publication
TK
Takahiro Kobayashi
Specialist
1 IgG4-related retroperitoneal fibrosis publication
NF
Naoya Fujita
Specialist
1 IgG4-related retroperitoneal fibrosis publication
AS
Akinori Sekizawa
Specialist
1 IgG4-related retroperitoneal fibrosis publication
PV
Perry Veras
SACRAMENTO, CA
Specialist
1 IgG4-related retroperitoneal fibrosis publication
MB
Maryam Bolouri
Specialist
1 IgG4-related retroperitoneal fibrosis publication
SG
Shashank Gupta
Specialist
1 IgG4-related retroperitoneal fibrosis publication
EA
Emad Allam
MAYWOOD, IL
Specialist
1 IgG4-related retroperitoneal fibrosis publication
LP
Liubov Petelytska
Specialist
1 IgG4-related retroperitoneal fibrosis publication
AN
Adriana Nikitina
Specialist
1 IgG4-related retroperitoneal fibrosis publication
OT
Oksana Tarasenko
Specialist
1 IgG4-related retroperitoneal fibrosis publication
WM
Wen Zhang, MD
Specialist
PI on 9 active trials1 IgG4-related retroperitoneal fibrosis publication
MM
Mark D Topazian, MD
ROCHESTER, MN
Specialist
PI on 1 active trial
AM
Arezou Khosroshahi, MD
ATLANTA, GA
Specialist
PI on 1 active trial1 IgG4-related retroperitoneal fibrosis publication
HD
Hui Gao, Doctor
Specialist
PI on 1 active trial
JZ
Jian Zhu
Specialist
PI on 1 active trial404 IgG4-related retroperitoneal fibrosis publications
EM
Etika Rathi, MDS
Specialist
PI on 1 active trial
CB
Carlo Buzio
Specialist
PI on 1 active trial
AD
Aline DECHANET
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to IgG4-related retroperitoneal fibrosis.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about IgG4-related retroperitoneal fibrosis

Disease timeline:

New recruiting trial: Early Discontinuation of Steroid Treatment in Negative FDG-PET/CT Patients With Idiopathic Retroperitoneal Fibrosis

A new clinical trial is recruiting patients for IgG4-related retroperitoneal fibrosis

New recruiting trial: A Prospective Cohort Study of IRPF in China

A new clinical trial is recruiting patients for IgG4-related retroperitoneal fibrosis

New recruiting trial: National Registry of IRPF in China

A new clinical trial is recruiting patients for IgG4-related retroperitoneal fibrosis

New recruiting trial: Study of Sirolimus in Idiopathic Retroperitoneal Fibrosis

A new clinical trial is recruiting patients for IgG4-related retroperitoneal fibrosis

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How do you know this is IgG4-related and not another cause of retroperitoneal fibrosis, such as cancer?,How much kidney damage has already occurred, and is it reversible?,What is the plan if my disease comes back after I stop steroids?,Are there clinical trials I might be eligible for?,How long will I need to be on treatment, and what are the long-term risks?,Should I see a urologist to check whether my ureters need a stent?,What symptoms should prompt me to call you or go to the emergency room?

Common questions about IgG4-related retroperitoneal fibrosis

What is IgG4-related retroperitoneal fibrosis?

IgG4-related retroperitoneal fibrosis (also called IgG4-RF or IgG4-related periaortitis/periarteritis) is a rare inflammatory disease where the immune system mistakenly triggers the buildup of scar-like tissue (fibrosis) in the retroperitoneum — the space behind the abdominal cavity that contains the kidneys, major blood vessels, and the tubes that carry urine from the kidneys to the bladder (ureters). This disease belongs to a broader family of conditions called IgG4-related disease (IgG4-RD), in which a type of immune protein called IgG4 plays a central role in causing inflammation and scarr

How is IgG4-related retroperitoneal fibrosis inherited?

IgG4-related retroperitoneal fibrosis follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does IgG4-related retroperitoneal fibrosis typically begin?

Typical onset of IgG4-related retroperitoneal fibrosis is adult. Age of onset can vary across affected individuals.

Are there clinical trials for IgG4-related retroperitoneal fibrosis?

Yes — 5 recruiting clinical trials are currently listed for IgG4-related retroperitoneal fibrosis on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat IgG4-related retroperitoneal fibrosis?

23 specialists and care centers treating IgG4-related retroperitoneal fibrosis are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.