Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:567552N04.8
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy (sometimes called SRNS with second-line response) is a rare kidney disease. In nephrotic syndrome, the tiny filtering units in the kidneys — called glomeruli — become damaged and leaky. This causes large amounts of protein to spill into the urine instead of staying in the blood where it belongs. When this happens, the body loses important proteins, leading to swelling (especially in the legs, ankles, and around the eyes), low protein levels in the blood, and high cholesterol. What makes this specific form unique is a two-part pattern: first, the disease does not respond to steroids (the usual first treatment for nephrotic syndrome). This is called steroid resistance. However, unlike some other steroid-resistant forms, this condition does respond to second-line immunosuppressive medicines — drugs that calm down an overactive immune system, such as calcineurin inhibitors like cyclosporine or tacrolimus. Symptoms include significant swelling, foamy urine (from protein), fatigue, reduced urine output, and weight gain from fluid buildup. Because the cause is not fully understood (hence 'idiopathic'), management focuses on finding the right combination of immune-suppressing medicines. With the right treatment, many patients can achieve remission and protect their kidneys from long-term damage.

Also known as:

Key symptoms:

Severe swelling in the legs, ankles, feet, and around the eyesFoamy or frothy urine caused by excess proteinUnexplained weight gain from fluid buildup in the bodyLow levels of protein in the bloodHigh cholesterol and high triglyceridesFatigue and low energyReduced amount of urinePuffy abdomen from fluid accumulationIncreased risk of infections due to loss of immune proteinsIncreased risk of blood clots

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy.

View clinical trials →

No actively recruiting trials found for Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy community →

No specialists are currently listed for Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapyForum →

No community posts yet. Be the first to share your experience with Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy.

Start the conversation →

Latest news about Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy

No recent news articles for Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which second-line immunosuppressive medicine do you recommend for me, and why?,Should I have genetic testing to find out if there is a genetic cause for my nephrotic syndrome?,How will we know if the treatment is working, and how long before we expect to see improvement?,What are the long-term side effects of the medicines I will be taking, and how will we monitor for them?,What are the signs of a relapse, and what should I do if I think I am having one?,Are there any clinical trials or newer treatments I should know about?,What dietary changes should I make, and should I see a kidney dietitian?

Common questions about Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy

What is Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy?

Idiopathic steroid-resistant nephrotic syndrome with sensitivity to second-line immunosuppressive therapy (sometimes called SRNS with second-line response) is a rare kidney disease. In nephrotic syndrome, the tiny filtering units in the kidneys — called glomeruli — become damaged and leaky. This causes large amounts of protein to spill into the urine instead of staying in the blood where it belongs. When this happens, the body loses important proteins, leading to swelling (especially in the legs, ankles, and around the eyes), low protein levels in the blood, and high cholesterol. What makes t