Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome

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ORPHA:69088OMIM:300291Q78.2
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Overview

Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome, also known as HED-ID-OL or OLEDAID syndrome, is a very rare inherited condition that affects multiple body systems at the same time. It is caused by changes (mutations) in the IKBKG gene, which is also called NEMO. This gene plays a key role in helping the immune system fight infections and in the normal development of skin, teeth, hair, and bones. People with this condition typically have reduced sweating (hypohidrosis), which makes it hard for the body to cool itself down. They also have a weakened immune system, making them much more likely to get serious bacterial, viral, and fungal infections. Bones can become abnormally dense and thick (osteopetrosis), which sounds like it would make them stronger, but actually makes them more fragile and prone to fractures. Swelling caused by fluid buildup in the limbs (lymphedema) is another common feature. Other signs include sparse hair, missing or unusually shaped teeth, and dry skin. Because so many body systems are involved, care requires a team of specialists. There is no cure at this time, but treatments focus on preventing infections, managing symptoms, and improving quality of life. In some cases, bone marrow transplant has been explored to address the immune deficiency.

Also known as:

Key symptoms:

Reduced or absent sweating, making it hard to stay coolFrequent and severe infections (bacterial, viral, fungal)Abnormally dense, thick bones (osteopetrosis) that are prone to fracturesSwelling in the arms or legs due to fluid buildup (lymphedema)Sparse or thin hairMissing, small, or cone-shaped teethDry or scaly skinDistinctive facial features such as a prominent forehead and sunken nose bridgeRecurrent lung infections or pneumoniaAnemia or low blood cell counts related to bone marrow problems

Inheritance

X-linked recessive

Carried on the X chromosome; typically affects males more than females

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome.

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No actively recruiting trials found for Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome at this time.

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No specialists are currently listed for Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome.

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Community

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Latest news about Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome

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Caregiver Resources

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Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific mutation was found in the IKBKG gene, and what does it mean for my child's prognosis?,Should we consider bone marrow transplantation, and what are the risks and benefits for our situation?,What infections should we be most worried about, and what preventive treatments are recommended?,How do we manage overheating safely at home and at school?,What specialists should be part of our care team, and how often should we see each one?,Are there any clinical trials or research studies we should know about?,What should we do in an emergency, and when should we go straight to the hospital?

Common questions about Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome

What is Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome?

Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome, also known as HED-ID-OL or OLEDAID syndrome, is a very rare inherited condition that affects multiple body systems at the same time. It is caused by changes (mutations) in the IKBKG gene, which is also called NEMO. This gene plays a key role in helping the immune system fight infections and in the normal development of skin, teeth, hair, and bones. People with this condition typically have reduced sweating (hypohidrosis), which makes it hard for the body to cool itself down. They also have a weakened immune

How is Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome inherited?

Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome follows a x-linked recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome typically begin?

Typical onset of Hypohidrotic ectodermal dysplasia-immunodeficiency-osteopetrosis-lymphedema syndrome is neonatal. Age of onset can vary across affected individuals.