Hereditary optic neuropathy

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ORPHA:98671
Who is this for?
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1Active trials3Specialists8Treatment centers

Where are you in your journey?

ℹ
UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Orphanet ↗NORD ↗

FDA & Trial Timeline

2 events
Apr 2026Novel Technologies to Measure Vision-related Quality of Life

Nisha Nixon

TrialNOT YET RECRUITING
Jun 2021Gene Therapy Clinical Trial for the Treatment Of Leber's HereDitary Optic Neuropathy

Wuhan Neurophth Biotechnology Limited Company — PHASE2, PHASE3

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Hereditary optic neuropathy.

1 clinical trialare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

1 recruitingView all trials with filters →

Specialists

3 foundView all specialists →
SM
Stefano C Previtali, MD
Milan
Specialist

Rare Disease Specialist

HT
Henry Tseng
DURHAM, NC
Specialist
PI on 1 active trial
FM
Felipe A Medeiros
MIAMI, FL
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center ↗

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center ↗

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program ↗

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site ↗

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site ↗

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site ↗

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine ↗

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program ↗

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Hereditary optic neuropathy.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Hereditary optic neuropathy

Disease timeline:

New trial: Impact of Sensory, Motor and Vestibular Deficit on the Postural Stability of CMT Patients

Phase NA trial recruiting.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Hereditary optic neuropathy

Are there clinical trials for Hereditary optic neuropathy?

Yes — 1 recruiting clinical trial is currently listed for Hereditary optic neuropathy on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Hereditary optic neuropathy?

3 specialists and care centers treating Hereditary optic neuropathy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.