Hereditary Neutropenia

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Who is this for?
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1FDA treatments1Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Hereditary Neutropenia is treated with 1 medication in our database, including NYVEPRIA. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Pfizer. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Hereditary Neutropenia treatment below.

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

NORD ↗

Treatments

1 available

NYVEPRIA

pegfilgrastim-apgf· Pfizer

* Patient Copay Amount: As little as $0 per treatment for certain injectable or infusion medicines, and as little as $0 per month for oral treatments. * Maximum Annual Benefit Limit: Varies by produc

No actively recruiting trials found for Hereditary Neutropenia at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Hereditary Neutropenia community →

Specialists

1 foundView all specialists →
MM
Matthew M Hsieh, M.D.
Bethesda, Maryland
Specialist

Rare Disease Specialist

PI on 4 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Hereditary Neutropenia.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Hereditary Neutropenia

No recent news articles for Hereditary Neutropenia.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Hereditary Neutropenia

What is Hereditary Neutropenia?

Hereditary Neutropenia is treated with 1 medication in our database, including NYVEPRIA. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Pfizer. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Hereditary Neutropenia treatment below.

At what age does Hereditary Neutropenia typically begin?

Typical onset of Hereditary Neutropenia is neonatal. Age of onset can vary across affected individuals.

Which specialists treat Hereditary Neutropenia?

1 specialists and care centers treating Hereditary Neutropenia are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Hereditary Neutropenia?

1 FDA-approved treatment are currently tracked on UniteRare for Hereditary Neutropenia. See the treatments and support programs sections for copay assistance, eligibility, and contact details.