Hereditary Erythropoietic Porphyria

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1FDA treatments8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Hereditary Erythropoietic Porphyria is treated with 1 medication in our database, including SCENESSE. Medications are manufactured by Clinuvel. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Hereditary Erythropoietic Porphyria treatment below.

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

NORD ↗

Treatments

1 available

SCENESSE

afamelanotide· Clinuvel

* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Must have commercial or private health insurance; not valid for

No actively recruiting trials found for Hereditary Erythropoietic Porphyria at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Hereditary Erythropoietic Porphyria community →

No specialists are currently listed for Hereditary Erythropoietic Porphyria.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Hereditary Erythropoietic Porphyria.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Hereditary Erythropoietic Porphyria

No recent news articles for Hereditary Erythropoietic Porphyria.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Hereditary Erythropoietic Porphyria

What is Hereditary Erythropoietic Porphyria?

Hereditary Erythropoietic Porphyria is treated with 1 medication in our database, including SCENESSE. Medications are manufactured by Clinuvel. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Hereditary Erythropoietic Porphyria treatment below.

How is Hereditary Erythropoietic Porphyria inherited?

Hereditary Erythropoietic Porphyria follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Hereditary Erythropoietic Porphyria typically begin?

Typical onset of Hereditary Erythropoietic Porphyria is childhood. Age of onset can vary across affected individuals.

What treatment and support options exist for Hereditary Erythropoietic Porphyria?

1 FDA-approved treatment and 1 patient support program are currently tracked on UniteRare for Hereditary Erythropoietic Porphyria. See the treatments and support programs sections for copay assistance, eligibility, and contact details.