Treatments for Hereditary ATTR amyloidosis
FDA-approved drugs, patient assistance programs, and travel grants tracked on UniteRare for this condition.
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Treatment data is extracted from FDA drug labels, DailyMed, and openFDA through automated and AI-assisted pipelines that read both structured records and unstructured label text.
Report missing dataFDA-approved treatments (6)
- VyndaqelTAFAMIDIS MEGLUMINEPfizer Laboratories Div Pfizer Inc
- WAINUAEPLONTERSENAstraZeneca Pharmaceuticals LP
- OnpattroPATISIRANAlnylam Pharmaceuticals, Inc.
- AMVUTTRAVUTRISIRANAlnylam Pharmaceuticals, Inc.
- AttrubyACORAMIDIS HYDROCHLORIDEBridgeBio Pharma, Inc.Approved Nov 2024
- TegsediinotersenIonis/AstraZenecaApproved Oct 2018
Patient support programs (7)
Copay cards, manufacturer assistance, and foundation grants. Verification status shown on each card.
Vyndaqel
Pfizer Laboratories Div Pfizer Inc
Unverified — confirm before calling
copay card
copay assistancePatient Assistance
Accepting applications
WAINUA
AstraZeneca Pharmaceuticals LP
WAINUA Patient Support (AZ&Me)
Link unavailable
Patient Assistance
Manufacturer Program
Accepting applications
1-800-236-9933Call for current details
The Assistance Fund — Hereditary transthyretin-mediated amyloidosis
The Assistance Fund
Hereditary transthyretin-mediated amyloidosis
Verified 32d ago
Foundation Grant
foundation grant
Accepting applications
Tegsedi
Ionis/AstraZeneca
Unverified — confirm before calling
copay card
copay assistancePatient Assistance
Accepting applications
WAINUA
AstraZeneca Pharmaceuticals LP
WAINUA Patient Support (AZ&Me)
Patient Assistance
Manufacturer Program
Accepting applications
Attruby
BridgeBio Pharma, Inc.
Attruby — Contact BridgeBio Pharma, Inc.
Unverified — confirm before calling
Patient Assistance
Manufacturer Program
Accepting applications
Vyndaqel
Pfizer Laboratories Div Pfizer Inc
Vyndaqel Patient Support (Pfizer Patient Assistance)
Verified 9d ago
Patient Assistance
Manufacturer Program
Accepting applications