Clinical trials for Glycogen storage disease due to glucose-6-phosphatase deficiency
2 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPHASE1, PHASE2NCT06735755A Phase 1/2, Dose-Exploration Study to Evaluate the Safety and Efficacy of BEAM-301 in Patients With Glycogen Storage Disease Type Ia (GSDIa)Beam Therapeutics Inc.
- RECRUITINGNCT06636383Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring ProgramUltragenyx Pharmaceutical Inc · PI: Medical Director