Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome

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ORPHA:488613OMIM:616973F84.8
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8Treatment centers

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Overview

Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome (sometimes referred to by its Orphanet code ORPHA:488613) is a rare genetic condition that affects brain development and the eyes. Children with this syndrome typically show signs early in life, including delays in reaching milestones like sitting, walking, and talking. The brain does not develop in the usual way, which leads to intellectual disability that can range from mild to severe. The condition also affects the eyes and the nerves that control vision, which is why it is called a 'neuro-ophthalmological' syndrome. This can cause problems with eye movement, vision loss, or abnormal appearance of the optic nerve. Seizures are another major feature, meaning the brain sometimes sends abnormal electrical signals that cause episodes of shaking, staring, or loss of awareness. Right now, there is no cure for this syndrome. Treatment focuses on managing symptoms — for example, anti-seizure medications to reduce seizures, glasses or other supports for vision problems, and therapies like speech, physical, and occupational therapy to help children reach their potential. A team of specialists usually works together to support affected individuals and their families.

Key symptoms:

Delayed development in areas like walking, talking, and learningIntellectual disability ranging from mild to severeSeizures or epilepsyAbnormal eye movements or difficulty controlling eye movementVision problems or vision lossAbnormal appearance of the optic nerve (the nerve connecting the eye to the brain)Low muscle tone (floppy muscles) in infancyDifficulty with coordination and balanceSpeech and language delaysBehavioral challenges

Clinical phenotype terms (29)— hover any for plain English
Limb hypertoniaHP:0002509Impaired smooth pursuitHP:0007772EEG with generalized epileptiform dischargesHP:0011198
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome.

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No actively recruiting trials found for Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome at this time.

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No specialists are currently listed for Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which specific gene or genetic change is causing this condition in my child, and what does that mean for our family?,What type of seizures does my child have, and which medication is most likely to help?,What vision problems should I watch for, and how often should my child see an eye specialist?,What therapies do you recommend, and how early should we start?,Are there any clinical trials or research studies we could participate in?,What should I do if my child has a prolonged seizure at home?,What educational and community support services are available for my child?

Common questions about Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome

What is Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome?

Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome (sometimes referred to by its Orphanet code ORPHA:488613) is a rare genetic condition that affects brain development and the eyes. Children with this syndrome typically show signs early in life, including delays in reaching milestones like sitting, walking, and talking. The brain does not develop in the usual way, which leads to intellectual disability that can range from mild to severe. The condition also affects the eyes and the nerves that control vision, which is why it is called a 'n

How is Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome inherited?

Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome typically begin?

Typical onset of Global developmental delay-neuro-ophthalmological abnormalities-seizures-intellectual disability syndrome is infantile. Age of onset can vary across affected individuals.