Specialists for Gangliosidosis
33 physicians and care centers identified from ClinicalTrials.gov trial PIs, PubMed publications, and the NPPES NPI registry.
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Specialists are identified from ClinicalTrials.gov principal investigators, PubMed publications, and the NPI registry, then ranked through an automated scoring pipeline.
Report missing data- Maria T AcostaRare Disease / Clinical ResearchOffice of the Clinical Director and Medical Genetics BranchQC-verified 3
- Terence R Flotte, MDRare Disease / Clinical ResearchHorae Gene Therapy Center and The Li Weibo Institute for Rare Diseases ResearchWORCESTER, MAQC-verified 3
- Jean M JohnstonRare Disease / Clinical ResearchOffice of the Clinical Director and Medical Genetics BranchQC-verified 3
- Anne S MaguireRare Disease / Clinical ResearchAuburn University College of Veterinary MedicineQC-verified 2
- Meghan Blackwood, MA, BCBARare Disease / Clinical ResearchHorae Gene Therapy Center and The Li Weibo Institute for Rare Diseases ResearchMIAMISBURG, OHQC-verified 3
- Rauan KaiyrzhanovRare Disease / Clinical Researcheuromuscular Disorders Institute of NeurologyQC-verified 2
- Cynthia J Tifft, MDRare Disease / Clinical ResearchOffice of the Clinical Director and Medical Genetics BranchWASHINGTON, DCQC-verified 5
- Douglas R MartinRare Disease / Clinical ResearchCollege of Veterinary MedicineQC-verified 4
- Connor J LewisRare Disease / Clinical ResearchOffice of the Clinical Director and Medical Genetics BranchQC-verified 4
- Xuntian JiangRare Disease / Clinical ResearchWashington University School of MedicineQC-verified 3
- Zeynep Vardar, MDRare Disease / Clinical ResearchUniversity of Massachusetts Chan Medical SchoolFORT MYERS, FLQC-verified 3
- Eva-Maria RataiRare Disease / Clinical ResearchMassachusetts General Hospital and Harvard Medical SchoolQC-verified 3
- Allison M Keeler, RNRare Disease / Clinical ResearchHorae Gene Therapy Center and The Li Weibo Institute for Rare Diseases ResearchWENATCHEE, WAQC-verified 3
- Miguel Sena-EstevesRare Disease / Clinical ResearchHorae Gene Therapy Center and Li Weibo Institute for Rare Diseases ResearchQC-verified 3
- Paul Orchard, MD, MDRare Disease / Clinical ResearchUniversity of Minnesota Medical CenterMINNEAPOLIS, MNPI×15
- Florian Eichler, MD, MDRare Disease / Clinical ResearchMassachusetts General HospitalBOSTON, MAPI×4
- Adeline Vanderver, MDRare Disease SpecialistChildren's Hospital of PhiladelphiaLos Angeles, CaliforniaPI×4 1
- Jeanine R. Jarnes, PharmDRare Disease / Clinical ResearchUniversity of Minnesota - FairviewMINNEAPOLIS, MNPI×3
- Joe TR Clarke, MDRare Disease / Clinical ResearchThe Hospital for Sick Children, Toronto CanadaPI×1
- Joanne Kurtzberg, MD, M.DRare Disease / Clinical ResearchDuke UniversityDURHAM, NCPI×11
- Joe T Clarke, MDRare Disease / Clinical ResearchThe Hospital for Sick ChildrenPI×1
- Cynthia J Tifft, M.D.Rare Disease SpecialistNational Human Genome Research Institute (NHGRI)Bethesda, MarylandPI×2
- May Orfali, MDRare Disease / Clinical ResearchGemma BiotherapeuticsPI×3
- Anupam Sehgal, MBBSRare Disease SpecialistQueen's UniversityKingston, OntarioPI×1
- Terence Flotte, MD, MDRare Disease / Clinical ResearchUMass Chan Medical SchoolWORCESTER, MAPI×2
- Jeffrey Krischer, PhDRare Disease / Clinical ResearchUniversity of South FloridaPI×3
- Guillaume Sillon, MScRare Disease / Clinical ResearchMcGill University Health Centre/Research Institute of the McGill University Health CentrePI×1
- Mindy Leffler, MEdRare Disease / Clinical ResearchCasimir TrialsPI×1
- Can Ficicioglu, MD, PhD, M.DRare Disease / Clinical ResearchChildren's Hospital of PhiladelphiaPHILADELPHIA, PAPI×2
- Chester B. Whitley, PhD, MD, P.A.-CRare Disease / Clinical ResearchUniversity of MinnesotaLAS VEGAS, NVPI×1
- Erika De BoeverRare Disease / Clinical ResearchEDB Consulting3
- Bijan AlmassianExsar CorporationQC-verified PI×1
- Zhong-yu YuanSun Yat-sen UniversityQC-verified PI×1