Functional variant of Guillain-Barré syndrome

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ORPHA:231419
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4Active trials8Treatment centers

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Overview

Functional variant of Guillain-Barré syndrome (GBS) refers to a specific subtype within the broader group of Guillain-Barré syndrome conditions. Guillain-Barré syndrome is a disorder in which the body's immune system mistakenly attacks the peripheral nerves — the nerves outside the brain and spinal cord. This leads to weakness, numbness, and sometimes paralysis. The "functional variant" designation under Orphanet (code 231419) refers to particular clinical presentations of GBS that may not fit neatly into the most common forms (such as acute inflammatory demyelinating polyneuropathy or Miller Fisher syndrome) but still share the core features of immune-mediated nerve damage. Symptoms typically begin with tingling or weakness in the legs that can spread to the arms and upper body. In more severe cases, the weakness can progress to the point where patients have difficulty breathing, swallowing, or moving. Some patients experience significant pain, changes in heart rate or blood pressure, and problems with bladder or bowel function. The condition usually develops over days to a few weeks, often following an infection such as a stomach bug or respiratory illness. Treatment focuses on reducing the immune attack and supporting the body during recovery. The two main treatments are intravenous immunoglobulin (IVIg), which involves infusing antibodies from donated blood, and plasma exchange (plasmapheresis), which filters harmful antibodies from the blood. Supportive care in a hospital setting — including monitoring breathing and heart function — is critical during the acute phase. Most patients recover, though the timeline and completeness of recovery can vary widely.

Also known as:

Key symptoms:

Weakness in the legs that may spread upwardTingling or pins-and-needles sensation in hands and feetDifficulty walking or climbing stairsFacial weakness or droopingDifficulty swallowingDifficulty breathingPain in the back, legs, or armsRapid or irregular heartbeatBlood pressure changesBladder or bowel problemsNumbness or loss of sensationFatigue and exhaustionDouble vision or difficulty moving the eyes

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

FDA & Trial Timeline

7 events
Jan 2026Comparison of the Efficacy and Safety of Immunoadsorption and Intravenous Immunoglobulin for Guillain-Barre Syndrome

The First Affiliated Hospital of Zhengzhou University — NA

TrialNOT YET RECRUITING
Sep 2025An Open Label Clinical Study to Evaluate Tanruprubart (Also Commonly Known as ANX005) in Participants With Guillain-Barré Syndrome (FORWARD Study)

Annexon, Inc. — PHASE3

TrialRECRUITING
Aug 2025Noninvasive Support for Acute Respiratory Failure in Guillain-Barré Syndrome

Assiut University — NA

TrialNOT YET RECRUITING
Apr 2025Efgartigimod for the Treatment of Guillain-Barré Syndrome

Zhongming Qiu — PHASE2, PHASE3

TrialNOT YET RECRUITING
Feb 2025Early vs. Late Tracheostomy in Patients With Guillain -Barre Syndrome

Meir Medical Center

TrialRECRUITING
May 2023Ventilator Trigger Sensitivity Adjustment Versus Threshold Inspiratory Muscle Training on Arterial Blood Gases

Cairo University — NA

TrialRECRUITING
Mar 2021Firm Observational Clinical Unicenter Study on Guillain Barré Syndrome

University Hospital, Basel, Switzerland

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Functional variant of Guillain-Barré syndrome.

4 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

4 recruitingView all trials with filters →
Phase 31 trial
An Open Label Clinical Study to Evaluate Tanruprubart (Also Commonly Known as ANX005) in Participants With Guillain-Barré Syndrome (FORWARD Study)
Phase 3
Actively Recruiting
PI: Clinical Trials (Annexon, Inc.) · Sites: Scottsdale, Arizona; Orange, California +7 more · Age: 1285 yrs
N/A1 trial
Ventilator Trigger Sensitivity Adjustment Versus Threshold Inspiratory Muscle Training on Arterial Blood Gases
N/A
Actively Recruiting
PI: Elmasry (Cairo University) · Sites: Cairo · Age: 2055 yrs
Other2 trials
Early vs. Late Tracheostomy in Patients With Guillain -Barre Syndrome
Actively Recruiting
· Sites: Kfar Saba · Age: 1899 yrs
Firm Observational Clinical Unicenter Study on Guillain Barré Syndrome
Actively Recruiting
PI: Raoul Sutter, Prof. Dr. med. (Clinic for Intensive Care Medicine, University Hos) · Sites: Basel · Age: 1899 yrs

No specialists are currently listed for Functional variant of Guillain-Barré syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Functional variant of Guillain-Barré syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Questions for your doctor

Bring these to your next appointment

  • Q1.Which subtype of Guillain-Barré syndrome do I have, and how does that affect my treatment plan?,How severe is my case, and what is the expected timeline for recovery?,Which treatment do you recommend — IVIg or plasma exchange — and why?,What signs should I watch for that would require emergency medical attention?,What rehabilitation services will I need, and how soon should they start?,Are there any long-term complications I should be aware of?,What can I do to manage pain and fatigue during recovery?

Common questions about Functional variant of Guillain-Barré syndrome

What is Functional variant of Guillain-Barré syndrome?

Functional variant of Guillain-Barré syndrome (GBS) refers to a specific subtype within the broader group of Guillain-Barré syndrome conditions. Guillain-Barré syndrome is a disorder in which the body's immune system mistakenly attacks the peripheral nerves — the nerves outside the brain and spinal cord. This leads to weakness, numbness, and sometimes paralysis. The "functional variant" designation under Orphanet (code 231419) refers to particular clinical presentations of GBS that may not fit neatly into the most common forms (such as acute inflammatory demyelinating polyneuropathy or Miller

How is Functional variant of Guillain-Barré syndrome inherited?

Functional variant of Guillain-Barré syndrome follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Functional variant of Guillain-Barré syndrome?

Yes — 4 recruiting clinical trials are currently listed for Functional variant of Guillain-Barré syndrome on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.