FOXG1 syndrome

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ORPHA:561854OMIM:613454Q04.8
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17Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

FOXG1 syndrome is a rare brain development disorder caused by changes in the FOXG1 gene, which plays a key role in how the brain grows before and after birth. It is sometimes called congenital FOXG1 syndrome or FOXG1-related disorder. The condition affects the structure and function of the brain, leading to significant challenges with movement, communication, and learning. Most children with FOXG1 syndrome have severe intellectual disability, meaning they need lifelong support with daily activities. Many children also experience seizures, involuntary movements, and difficulties with feeding and swallowing. FOXG1 syndrome shares some features with Rett syndrome, and the two were once grouped together, but they are now recognized as separate conditions. Unlike classic Rett syndrome, FOXG1 syndrome often appears earlier in life — sometimes in the first few months — and tends to cause more severe symptoms from the start. Brain scans often show that the brain is smaller than usual or has structural differences. There is currently no cure for FOXG1 syndrome. Treatment focuses on managing symptoms, improving quality of life, and supporting development. This includes anti-seizure medications, physical therapy, occupational therapy, speech therapy, and nutritional support. A team of specialists is usually needed to provide the best care. Research into gene-based therapies is ongoing and offers hope for future treatments.

Also known as:

Key symptoms:

Severe intellectual disabilityLittle or no ability to speakSeizures (epilepsy)Involuntary repetitive hand movements or wringingLow muscle tone (floppy muscles) in infancyStiff or tight muscles (spasticity) over timeDifficulty walking or inability to walkFeeding and swallowing difficultiesSlow head growth (microcephaly)Poor eye contact or limited social interactionSleep disturbancesBreathing irregularitiesHyperkinetic movements (excessive, uncontrolled movements)Gastroesophageal refluxScoliosis (curved spine)

Clinical phenotype terms (49)— hover any for plain English
Paroxysmal bursts of laughterHP:0000749
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for FOXG1 syndrome.

View clinical trials →

No actively recruiting trials found for FOXG1 syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the FOXG1 syndrome community →

Specialists

17 foundView all specialists →
NB
Nadia Bahi-Buisson
Specialist
2 FOXG1 syndrome publications
LW
Lee-Chin Wong
Specialist
2 FOXG1 syndrome publications
TV
Tanja Vogel
Specialist
2 FOXG1 syndrome publications
SJ
Shin Jeon
Specialist
5 FOXG1 syndrome publications
JP
Jaein Park
RIVERSIDE, CA
Specialist
5 FOXG1 syndrome publications
DS
Dongjun Shin
Specialist
5 FOXG1 syndrome publications
LL
Liwen Li
Specialist
5 FOXG1 syndrome publications
SL
Soo-Kyung Lee
Specialist
5 FOXG1 syndrome publications
JL
Jae W Lee
Specialist
4 FOXG1 syndrome publications
JM
Ji Hwan Moon
Specialist
3 FOXG1 syndrome publications
HO
Holly O'Shea
Specialist
3 FOXG1 syndrome publications
IA
Ipek Akol
Specialist
2 FOXG1 syndrome publications
FG
Fabian Gather
Specialist
2 FOXG1 syndrome publications
KK
Kopika Kuhathaas
Specialist
2 FOXG1 syndrome publications
AM
Alan K Percy, MD
BIRMINGHAM, AL
Specialist
PI on 2 active trials1 FOXG1 syndrome publication
JP
Jeffrey L Neul, MD, PhD
NASHVILLE, TN
Specialist
PI on 2 active trials
EB
Elise Brimble
PALO ALTO, CA
Specialist
4 FOXG1 syndrome publications

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to FOXG1 syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about FOXG1 syndrome

No recent news articles for FOXG1 syndrome.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What type of FOXG1 gene change does my child have, and does it affect the expected severity of symptoms?,What is the best anti-seizure medication plan for my child, and what should I do if a seizure lasts too long?,Is my child a candidate for a ketogenic diet to help with seizure control?,What therapies (physical, occupational, speech) should my child be receiving, and how often?,Are there any clinical trials or research studies for FOXG1 syndrome that my child might be eligible for?,How do I access augmentative and alternative communication (AAC) tools to help my child communicate?,What support services and caregiver resources are available in our area?

Common questions about FOXG1 syndrome

What is FOXG1 syndrome?

FOXG1 syndrome is a rare brain development disorder caused by changes in the FOXG1 gene, which plays a key role in how the brain grows before and after birth. It is sometimes called congenital FOXG1 syndrome or FOXG1-related disorder. The condition affects the structure and function of the brain, leading to significant challenges with movement, communication, and learning. Most children with FOXG1 syndrome have severe intellectual disability, meaning they need lifelong support with daily activities. Many children also experience seizures, involuntary movements, and difficulties with feeding an

How is FOXG1 syndrome inherited?

FOXG1 syndrome follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does FOXG1 syndrome typically begin?

Typical onset of FOXG1 syndrome is infantile. Age of onset can vary across affected individuals.

Which specialists treat FOXG1 syndrome?

17 specialists and care centers treating FOXG1 syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.