FGFR2-related bent bone dysplasia

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:313855OMIM:614592M85.8
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

FGFR2-related bent bone dysplasia is an extremely rare and severe skeletal disorder that affects bone development before birth. It is also known as bent bone dysplasia syndrome or FGFR2-related bent bone dysplasia syndrome. This condition is caused by specific mutations in the FGFR2 gene, which plays an important role in how bones grow and form during fetal development. Babies with this condition are typically identified before or at birth because of distinctive features including bent or bowed long bones (the bones in the arms and legs), underdeveloped bones in the skull (cranial hypomineralization), and unusual facial features such as a flat midface and low-set ears. The ribcage may also be small or abnormally shaped, which can cause serious breathing difficulties. Other features may include prematurely fused skull bones (craniosynostosis) and overall poor bone mineralization. Unfortunately, this condition is very severe, and most affected babies do not survive the newborn period due to breathing problems related to the small chest and underdeveloped lungs. There is currently no cure or specific treatment for this condition. Care is focused on comfort and supportive measures. Genetic counseling is important for affected families to understand the risk of recurrence in future pregnancies.

Also known as:

Key symptoms:

Bent or bowed long bones in the arms and legsPoorly mineralized skull bonesSmall or narrow chestFlat midfaceLow-set earsPremature fusion of skull bones (craniosynostosis)Underdeveloped lungsSevere breathing difficulties at birthShort limbsPoor overall bone mineralizationAbnormal rib shapeUnusual head shapePrenatal growth restriction

Clinical phenotype terms (27)— hover any for plain English
MegalocorneaHP:0000485Natal toothHP:0000695Short claviclesHP:0000894Bell-shaped thoraxHP:0001591Extramedullary hematopoiesisHP:0001978Hypoplastic ischiaHP:0003175Coronal craniosynostosisHP:0004440Overfolding of the superior helicesHP:0004453Decreased calvarial ossificationHP:0005474Early-onset non-progressive night blindnessHP:0007642Clitoral hypertrophyHP:0008665Steep acetabular roofHP:0010455
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for FGFR2-related bent bone dysplasia.

View clinical trials →

No actively recruiting trials found for FGFR2-related bent bone dysplasia at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the FGFR2-related bent bone dysplasia community →

No specialists are currently listed for FGFR2-related bent bone dysplasia.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to FGFR2-related bent bone dysplasia.

Search all travel grants →NORD Financial Assistance ↗

Community

Open FGFR2-related bent bone dysplasiaForum →

No community posts yet. Be the first to share your experience with FGFR2-related bent bone dysplasia.

Start the conversation →

Latest news about FGFR2-related bent bone dysplasia

No recent news articles for FGFR2-related bent bone dysplasia.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How certain is the diagnosis based on the current imaging or genetic test results?,What can we expect during the pregnancy and at delivery?,What comfort care and palliative care options are available for our baby?,Is genetic counseling available to help us understand the risk for future pregnancies?,Was this caused by a new mutation, or could other family members carry it?,What emotional and psychological support services are available for our family?,Can you connect us with other families who have experienced a similar diagnosis?

Common questions about FGFR2-related bent bone dysplasia

What is FGFR2-related bent bone dysplasia?

FGFR2-related bent bone dysplasia is an extremely rare and severe skeletal disorder that affects bone development before birth. It is also known as bent bone dysplasia syndrome or FGFR2-related bent bone dysplasia syndrome. This condition is caused by specific mutations in the FGFR2 gene, which plays an important role in how bones grow and form during fetal development. Babies with this condition are typically identified before or at birth because of distinctive features including bent or bowed long bones (the bones in the arms and legs), underdeveloped bones in the skull (cranial hypomineral

How is FGFR2-related bent bone dysplasia inherited?

FGFR2-related bent bone dysplasia follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does FGFR2-related bent bone dysplasia typically begin?

Typical onset of FGFR2-related bent bone dysplasia is neonatal. Age of onset can vary across affected individuals.