Familial osteodysplasia, Anderson type

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:2769OMIM:259250Q87.5
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Familial osteodysplasia, Anderson type, is an extremely rare inherited bone disorder that affects how bones and other tissues develop. This condition is sometimes also called Anderson-type familial osteodysplasia. It was first described in a small number of families and involves abnormal bone formation (osteodysplasia) along with other features that can affect multiple body systems. People with this condition typically show skeletal abnormalities that may include unusual bone shape, thinning of bones, and changes in the skull and facial bones. Additional features can include skin abnormalities, dental problems, and in some cases, hearing difficulties. The severity of symptoms can vary even among members of the same family. Because this disease is so rare, there is very limited information about its full range of symptoms and long-term outcomes. There is currently no specific cure or targeted treatment. Management focuses on addressing individual symptoms as they arise, which may include orthopedic care for bone problems, dental treatment, and monitoring for complications. Patients benefit from a team of specialists who can coordinate care across the different body systems that may be affected.

Key symptoms:

Abnormal bone shape and structureThinning or fragile bonesUnusual facial featuresSkull bone abnormalitiesDental problems or missing teethSkin changes or abnormalitiesHearing loss or hearing difficultiesShort stature or growth delaysJoint stiffness or limited joint movementNail abnormalities

Clinical phenotype terms (31)— hover any for plain English
Abnormal midface morphologyHP:0000309Abnormal earlobe morphologyHP:0000363Tooth malpositionHP:0000692Increased susceptibility to fracturesHP:0002659Long noseHP:0003189Aplasia/hypoplasia of the femurHP:0005613Failure of eruption of permanent teethHP:0006352
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Familial osteodysplasia, Anderson type.

View clinical trials →

No actively recruiting trials found for Familial osteodysplasia, Anderson type at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Familial osteodysplasia, Anderson type community →

No specialists are currently listed for Familial osteodysplasia, Anderson type.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Familial osteodysplasia, Anderson type.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Familial osteodysplasia, Anderson typeForum →

No community posts yet. Be the first to share your experience with Familial osteodysplasia, Anderson type.

Start the conversation →

Latest news about Familial osteodysplasia, Anderson type

No recent news articles for Familial osteodysplasia, Anderson type.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How severe is my child's bone involvement, and what complications should I watch for?,Should we pursue genetic testing, and what might it tell us?,How often should we schedule skeletal X-rays and hearing tests?,Are there any activities my child should avoid to protect their bones?,What dental specialists should be involved in my child's care?,Is there any ongoing research or clinical trials for this condition?,What is the expected long-term outlook for someone with this condition?

Common questions about Familial osteodysplasia, Anderson type

What is Familial osteodysplasia, Anderson type?

Familial osteodysplasia, Anderson type, is an extremely rare inherited bone disorder that affects how bones and other tissues develop. This condition is sometimes also called Anderson-type familial osteodysplasia. It was first described in a small number of families and involves abnormal bone formation (osteodysplasia) along with other features that can affect multiple body systems. People with this condition typically show skeletal abnormalities that may include unusual bone shape, thinning of bones, and changes in the skull and facial bones. Additional features can include skin abnormalitie

How is Familial osteodysplasia, Anderson type inherited?

Familial osteodysplasia, Anderson type follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Familial osteodysplasia, Anderson type typically begin?

Typical onset of Familial osteodysplasia, Anderson type is childhood. Age of onset can vary across affected individuals.