Familial episodic pain syndrome with predominantly upper body involvement

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ORPHA:391389OMIM:615040M79.6
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Overview

Familial episodic pain syndrome with predominantly upper body involvement is an extremely rare inherited condition that causes repeated episodes of intense pain, mainly affecting the upper parts of the body such as the arms, shoulders, chest, and sometimes the neck and jaw. The pain episodes typically begin in early childhood and can be triggered by factors such as cold weather, physical exertion, fatigue, or illness. During an episode, the pain can be severe and debilitating, often lasting from minutes to hours or even days. Between episodes, affected individuals usually feel normal and do not have ongoing pain. This condition belongs to a group of disorders known as familial episodic pain syndromes, which are caused by changes in genes that control how nerve cells send pain signals. Specifically, this form is linked to mutations in the TRPA1 gene, which encodes a protein involved in sensing pain and temperature. The faulty protein makes pain-sensing nerves overly excitable, leading to episodes of pain without any tissue damage. There is currently no cure for this condition. Treatment focuses on managing pain during episodes and trying to prevent triggers. Pain relief medications such as nonsteroidal anti-inflammatory drugs (NSAIDs) or other analgesics may be used, though responses to treatment can vary. Some patients find that avoiding known triggers helps reduce the frequency and severity of episodes. Because the condition is so rare, treatment approaches are often individualized based on each patient's experience.

Key symptoms:

Episodes of severe pain in the upper bodyPain in the arms and shouldersChest pain during episodesPain in the neck or jaw areaPain triggered by cold temperaturesPain triggered by physical exertion or fatiguePain triggered by fasting or hungerEpisodes that come and go with pain-free intervalsSweating during pain episodesFlushing or redness of the skin during episodesStiffness in affected areas during episodesDifficulty using arms or upper body during episodes

Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Familial episodic pain syndrome with predominantly upper body involvement.

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No actively recruiting trials found for Familial episodic pain syndrome with predominantly upper body involvement at this time.

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No specialists are currently listed for Familial episodic pain syndrome with predominantly upper body involvement.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Familial episodic pain syndrome with predominantly upper body involvement.

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Community

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Caregiver Resources

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Family & Caregiver Grants

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Social Security Disability

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Questions for your doctor

Bring these to your next appointment

  • Q1.What triggers should my family and I try to avoid to reduce pain episodes?,What pain medications are safest and most effective for this condition?,Are there any new treatments or clinical trials we should know about?,Should other family members be tested for the TRPA1 gene mutation?,How can we best manage pain episodes at home versus when should we seek emergency care?,Will the episodes change in frequency or severity as my child grows older?,Can you refer us to a pain management specialist experienced with rare genetic pain conditions?

Common questions about Familial episodic pain syndrome with predominantly upper body involvement

What is Familial episodic pain syndrome with predominantly upper body involvement?

Familial episodic pain syndrome with predominantly upper body involvement is an extremely rare inherited condition that causes repeated episodes of intense pain, mainly affecting the upper parts of the body such as the arms, shoulders, chest, and sometimes the neck and jaw. The pain episodes typically begin in early childhood and can be triggered by factors such as cold weather, physical exertion, fatigue, or illness. During an episode, the pain can be severe and debilitating, often lasting from minutes to hours or even days. Between episodes, affected individuals usually feel normal and do no

How is Familial episodic pain syndrome with predominantly upper body involvement inherited?

Familial episodic pain syndrome with predominantly upper body involvement follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Familial episodic pain syndrome with predominantly upper body involvement typically begin?

Typical onset of Familial episodic pain syndrome with predominantly upper body involvement is childhood. Age of onset can vary across affected individuals.