Embryonal tumor with multilayered rosettes

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ORPHA:656417C71.9
Who is this for?
Show terms as
1FDA treatments2Active trials44Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

Orphanet ↗NORD ↗

FDA & Trial Timeline

4 events
May 2025Integrated Analysis of Therapy Response and Resistence in Embryonal Tumors and Gliomas

University Hospital Regensburg

TrialNOT YET RECRUITING
Mar 2025Embryonal Tumor With Multilayered Rosettes

University of California, San Francisco — PHASE2

TrialRECRUITING
Jul 2020ETMR One: An International Registry and Research Platform for Children With Embryonal Tumor With Multilayer Rosettes

Hackensack Meridian Health

TrialRECRUITING
Nov 2018

VITRAKVI: FDA approved

VITRAKVI® is indicated for the treatment of adult and pediatric patients with solid tumors that have a neurotrophic receptor tyrosine kinase (NTRK) gene fusion without a known acquired resistance mutation; are metastatic or where surgical resection is likely to result in severe morbidity; and have no satisfactory alternative treatments or that have progressed following treatment.

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

VITRAKVI

larotrectinib· Bayer HealthCare Pharmaceuticals Inc.Orphan Drug
VITRAKVI� is indicated for the treatment of adult and pediatric patients with solid tumors that have a neurotrophic receptor tyrosine kinase (NTRK) gene fusion without a known acquired resistance mu

VITRAKVI� is indicated for the treatment of adult and pediatric patients with solid tumors that have a neurotrophic receptor tyrosine kinase (NTRK) gene fusion without a known acquired resistance mutation; are metastatic or where surgical resection is likely to result in severe morbidity; and have no satisfactory alternative treatments or that have progressed following treatment.

Clinical Trials

2 recruitingView all trials with filters →
Phase 21 trial
Embryonal Tumor With Multilayered Rosettes
Phase 2
Actively Recruiting
PI: Sabine Mueller, MD, PhD, MAS (University of California, San Francisco) · Sites: Birmingham, Alabama; San Francisco, California +4 more
Other1 trial
ETMR One: An International Registry and Research Platform for Children With Embryonal Tumor With Multilayer Rosettes
Actively Recruiting
PI: Derek Hanson, MD (Hackensack Meridian Health) · Sites: Hackensack, New Jersey

Specialists

Showing 25 of 44View all specialists →
KC
Karan R Chadda
Specialist
1 Embryonal tumor with multilayered rosettes publication
PP
Poe Phyu
Specialist
1 Embryonal tumor with multilayered rosettes publication
ML
Mercedes Llempén-López
Specialist
1 Embryonal tumor with multilayered rosettes publication
SK
Sara Khan
Specialist
1 Embryonal tumor with multilayered rosettes publication
AH
Annie Huang
Specialist
2 Embryonal tumor with multilayered rosettes publications
PS
Palma Solano-Páez
Specialist
1 Embryonal tumor with multilayered rosettes publication
BP
Barry Pizer
Specialist
1 Embryonal tumor with multilayered rosettes publication
KA
Kieren Allinson
Specialist
1 Embryonal tumor with multilayered rosettes publication
TJ
Thomas S Jacques
MAPLEWOOD, MN
Specialist
1 Embryonal tumor with multilayered rosettes publication
DA
Dilys Addy
Specialist
1 Embryonal tumor with multilayered rosettes publication
HL
Holly Lindsay
ALBUQUERQUE, NM
Specialist
1 Embryonal tumor with multilayered rosettes publication
JT
Jamie Trotman
Specialist
1 Embryonal tumor with multilayered rosettes publication
PT
Patrick Tarpey
CHICAGO, IL
Specialist
1 Embryonal tumor with multilayered rosettes publication
CE
Craig Erker
CINCINNATI, OH
Specialist
1 Embryonal tumor with multilayered rosettes publication
GH
Gail Horan
Specialist
1 Embryonal tumor with multilayered rosettes publication
NM
Nancy D. Perrier, MD
HOUSTON, TX
Specialist
PI on 7 active trials
RS
Ralph Salloum
BOSTON, MA
Specialist
PI on 2 active trials4 Embryonal tumor with multilayered rosettes publications
HM
Helen E Heslop, MD
HOUSTON, TX
Specialist
PI on 6 active trials
SL
Sarah E Leary
SEATTLE, WA
Specialist
PI on 2 active trials4 Embryonal tumor with multilayered rosettes publications
BM
Brian Kushner, MD
NEW YORK, NY
Specialist
PI on 8 active trials
SP
Stanislaw R. Burzynski, MD, PhD
HOUSTON, TX
Specialist
PI on 29 active trials
MI
Meredith S Irwin
CINCINNATI, OH
Specialist
PI on 1 active trial
SM
Sabine Mueller, MD, PhD, MAS
SAN FRANCISCO, CA
Specialist
PI on 8 active trials
SM
Susan K. Parsons, MD, MRP
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Embryonal tumor with multilayered rosettes.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Embryonal tumor with multilayered rosettes

Disease timeline:

New recruiting trial: Embryonal Tumor With Multilayered Rosettes

A new clinical trial is recruiting patients for Embryonal tumor with multilayered rosettes

New recruiting trial: CSIMEMPHIS: Long-term Follow-up of Medulloblastoma Survivors That Received Craniospinal Irradiation

A new clinical trial is recruiting patients for Embryonal tumor with multilayered rosettes

New recruiting trial: Relapsed and Progressive Sonic Hedgehog Medulloblastoma With U1 Mutation Registry Study

A new clinical trial is recruiting patients for Embryonal tumor with multilayered rosettes

New recruiting trial: A Study of Treatment for Medulloblastoma Using Sodium Thiosulfate to Reduce Hearing Loss

A new clinical trial is recruiting patients for Embryonal tumor with multilayered rosettes

New recruiting trial: DFMO as Maintenance Therapy for Molecular High/Very High Risk and Relapsed Medulloblastoma

A new clinical trial is recruiting patients for Embryonal tumor with multilayered rosettes

New recruiting trial: Metabolomics and Genetic Diagnosing Pancreatic Neuroendocrine Tumors in MEN1 Patients

A new clinical trial is recruiting patients for Embryonal tumor with multilayered rosettes

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Embryonal tumor with multilayered rosettes

Are there clinical trials for Embryonal tumor with multilayered rosettes?

Yes — 2 recruiting clinical trials are currently listed for Embryonal tumor with multilayered rosettes on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Embryonal tumor with multilayered rosettes?

25 specialists and care centers treating Embryonal tumor with multilayered rosettes are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Embryonal tumor with multilayered rosettes?

1 patient support program are currently tracked on UniteRare for Embryonal tumor with multilayered rosettes. See the treatments and support programs sections for copay assistance, eligibility, and contact details.