Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:247820OMIM:613573Q82.8
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome is a very rare inherited condition that affects the skin, hair, nails, and sweat glands — structures that all develop from the same layer of tissue in the embryo called the ectoderm. The name describes its three main features: ectodermal dysplasia (abnormal development of skin and related structures), pili torti (twisted hair shafts that are fragile and break easily), and cutaneous syndactyly (skin webbing between the fingers or toes). This condition is sometimes referred to simply by its Orphanet code ORPHA:247820, as it is so rare that no widely used shorthand name has been established. People with this syndrome are typically noticed at birth or in early infancy because of their unusual hair texture and the webbing between digits. The hair tends to be sparse, brittle, and twisted, which can cause it to break close to the scalp. Sweating may be reduced or absent, which means the body has trouble regulating temperature — this can be dangerous in hot weather. Nails may be thickened, ridged, or abnormally shaped. Skin between fingers or toes may be fused together, which can affect hand function depending on severity. There is currently no cure for this condition. Treatment focuses on managing individual symptoms — protecting the hair and skin, preventing overheating, and surgically separating fused digits when needed to improve function. A team of specialists is usually needed to provide the best care.

Key symptoms:

Twisted, fragile hair that breaks easily (pili torti)Sparse or thin hair on the scalpSkin webbing between fingers or toes (cutaneous syndactyly)Reduced or absent sweating (hypohidrosis or anhidrosis)Difficulty regulating body temperatureThickened, ridged, or abnormally shaped nailsDry or abnormal skin texturePossible dental abnormalities such as missing or malformed teethBrittle nails that break easily

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome.

View clinical trials →

No actively recruiting trials found for Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome community →

No specialists are currently listed for Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Ectodermal dysplasia-pili torti-cutaneous syndactyly syndromeForum →

No community posts yet. Be the first to share your experience with Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome.

Start the conversation →

Latest news about Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome

No recent news articles for Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What genetic tests should we do to confirm the diagnosis and identify the specific gene involved?,How serious is the risk of overheating, and what is our emergency plan if my child's temperature rises dangerously?,When is the best time to consider surgery for the webbed fingers or toes, and what outcomes can we expect?,Are there any other organ systems we should monitor that might be affected by this condition?,What accommodations should we request at school to keep my child safe?,What are the chances that future children could be affected, and should other family members be tested?,Are there any research studies or patient registries we can join to help advance understanding of this condition?

Common questions about Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome

What is Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome?

Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome is a very rare inherited condition that affects the skin, hair, nails, and sweat glands — structures that all develop from the same layer of tissue in the embryo called the ectoderm. The name describes its three main features: ectodermal dysplasia (abnormal development of skin and related structures), pili torti (twisted hair shafts that are fragile and break easily), and cutaneous syndactyly (skin webbing between the fingers or toes). This condition is sometimes referred to simply by its Orphanet code ORPHA:247820, as it is so rare

How is Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome inherited?

Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome typically begin?

Typical onset of Ectodermal dysplasia-pili torti-cutaneous syndactyly syndrome is neonatal. Age of onset can vary across affected individuals.