Dysostosis with brachydactyly

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ORPHA:69028
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Overview

Dysostosis with brachydactyly is a rare inherited bone and skeletal condition. The name describes its two main features: 'dysostosis' means abnormal bone formation, and 'brachydactyly' means unusually short fingers and toes. Together, these cause distinctive changes in the hands, feet, and sometimes other parts of the skeleton. This condition is also sometimes referred to in medical literature as a form of skeletal dysplasia involving short digits and bone malformation. People with this condition are typically born with noticeably short fingers and toes, and may also have other bone abnormalities affecting the face, skull, or limbs. The severity can vary from person to person. Some individuals may have mild features that mainly affect appearance and hand function, while others may experience more significant skeletal differences that affect movement and daily activities. There is currently no cure for dysostosis with brachydactyly. Treatment focuses on managing symptoms and improving quality of life. This may include physical therapy, occupational therapy, and in some cases surgery to improve hand or foot function. A team of specialists typically works together to support affected individuals throughout their lives.

Key symptoms:

Unusually short fingers and toes (brachydactyly)Abnormally shaped or fused bones in the hands and feetShort stature in some individualsFacial bone differences such as a flattened or unusual facial structureLimited range of motion in the fingers or toesAbnormal bone development in other parts of the skeletonNail abnormalities in some casesDifferences in the shape or size of the skull in some individuals

Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Dysostosis with brachydactyly.

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No actively recruiting trials found for Dysostosis with brachydactyly at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Dysostosis with brachydactyly community →

No specialists are currently listed for Dysostosis with brachydactyly.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Dysostosis with brachydactyly.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Dysostosis with brachydactyly

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which specific bones are affected in my child, and how will this change as they grow?,Is genetic testing recommended for our family, and what gene should be tested?,What therapies would help most with hand and finger function right now?,Will surgery ever be needed, and if so, when is the best time to consider it?,Are there any other parts of the body we should monitor for complications?,Are there patient registries or research studies we can join to help advance understanding of this condition?,What school or workplace accommodations should we request?

Common questions about Dysostosis with brachydactyly

What is Dysostosis with brachydactyly?

Dysostosis with brachydactyly is a rare inherited bone and skeletal condition. The name describes its two main features: 'dysostosis' means abnormal bone formation, and 'brachydactyly' means unusually short fingers and toes. Together, these cause distinctive changes in the hands, feet, and sometimes other parts of the skeleton. This condition is also sometimes referred to in medical literature as a form of skeletal dysplasia involving short digits and bone malformation. People with this condition are typically born with noticeably short fingers and toes, and may also have other bone abnormali

How is Dysostosis with brachydactyly inherited?

Dysostosis with brachydactyly follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Dysostosis with brachydactyly typically begin?

Typical onset of Dysostosis with brachydactyly is neonatal. Age of onset can vary across affected individuals.