Clinical trials for Dyskeratosis congenita
2 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPhase 1NCT06817590Nucleoside Therapy in Patients With Telomere Biology DisordersSuneet Agarwal · PI: Helen Reed, MD, MPH
- ACTIVE NOT RECRUITINGPhase 2NCT01659606Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis CongenitaBoston Children's Hospital · PI: Suneet Agarwal, MD, PHD